A Long-term Follow-up Study of Gaucher Disease

Status: Recruiting
Location: See location...
Study Type: Observational
SUMMARY

The study aims are to: a) identify the long-term natural history of Gaucher disease, b) evaluate long-term treatment efficacy of enzyme replacement therapy (ERT) and substrate reduction therapy (SRT), and c) identify potential long-term complications of this disorder. These aims will be accomplished through long-term record review of individuals with all three types of Gaucher disease.

Eligibility
Participation Requirements
Sex: All
View:

• Diagnosis of Gaucher Disease

Locations
United States
North Carolina
Duke University Medical Center
Recruiting
Durham
Contact Information
Primary
Janet Blount
janet.blount@duke.edu
919-681-7962
Time Frame
Start Date: June 12, 2017
Estimated Completion Date: January 2027
Participants
Target number of participants: 200
Sponsors
Leads: Duke University

This content was sourced from clinicaltrials.gov

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