A Long-term Study for the Outcome of Pompe Disease
Location: See location...
Study Type: Observational
Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.
Healthy Volunteers: No
• Confirm diagnosis with Pompe disease, is or is preparing receiving enzyme replacement therapy
National Taiwan University Hospital
Start Date: April 2007
Estimated Completion Date: December 2026
Target number of participants: 50
Related Therapeutic Areas
Leads: National Taiwan University Hospital