Prospective Clinical Assessment Study in Children With Achondroplasia: The PROPEL Trial

Status: Recruiting
Location: See all (20) locations...
Study Type: Observational
SUMMARY

This is a long-term, multi-center, observational study in children 2.5 to 10 years with achondroplasia (ACH). The objective is to evaluate growth, ACH-related medical complications and treatments of study participants. No study medication will be administered.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 2
Maximum Age: 10
Healthy Volunteers: No
View:

• Signed informed consent by study participant or parent(s) or legally authorized representative (LAR) and signed informed assent by the study participant (when applicable)

• Aged 2.5 to 10 years (inclusive) at study entry

• Diagnosis of ACH

• Ambulatory and able to stand without assistance

• Study participants and parent(s) or LAR(s) are willing and able to comply with study visits and study procedures

Locations
United States
California
Benioff Children's Hospital Oakland
Recruiting
Oakland
Delaware
Nemours Alfred I. Dupont Hospital for Children
Recruiting
Wilmington
Maryland
Johns Hopkins School of Medicine
Recruiting
Baltimore
Ohio
Cincinnati Children's Hospital
Recruiting
Cincinnati
Tennessee
Vanderbilt University Medical Center
Recruiting
Nashville
Texas
Cook's Children Medical Center
Recruiting
Dallas
Other Locations
Australia
Murdoch Children's Research Institute
Recruiting
Parkville
Canada
Stollery Children's Hospital
Recruiting
Edmonton
France
Hopital Femme Mere Enfant
Recruiting
Lyon
Hopital Necker-Enfants Malades
Recruiting
Paris
Hopital des Enfants
Recruiting
Toulouse
Spain
Vithas Hospital San Jose
Recruiting
Barcelona
Hospital Universitario La Paz
Recruiting
Madrid
Hospital Universitario Virgen de la Victoria
Recruiting
Málaga
United Kingdom
Birmingham Children's Hospital
Recruiting
Birmingham
Bristol Royal Hospital for Children
Recruiting
Bristol
Queen Elizabeth University Hospital
Recruiting
Glasgow
St. Thomas' Hospital
Recruiting
London
Manchester University Children's Hospital
Recruiting
Manchester
Sheffield Children's Hospital
Recruiting
Sheffield
Contact Information
Primary
QED Therapeutics
PROPELstudyinfo@QEDTX.com
1-877-280-5655
Time Frame
Start Date: August 12, 2019
Estimated Completion Date: June 2026
Participants
Target number of participants: 200
Authors
Howard Saal, Julie Hoover-Fong, Paul Harmatz, Helen McDevitt, Christine Burren, Jean Pierre Salles, John Phillips, Marc Nicolino, Fernando Santos Simarro, Melinda Irving, Jorge Knörr, Michael Bober, Peter Kannu, Paul Arundel, Vrinda Saraff, Antonio Leiva Gea, Ravi Savarirayan
Sponsors
Leads: QED Therapeutics, Inc.

This content was sourced from clinicaltrials.gov

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