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Condition

Adrenoleukodystrophy

Symptoms, Doctors, Treatments, Research & More

Latest Research

Latest Advance
Study
  • Condition: Cerebral Adrenoleukodystrophy
  • Journal: Stem cells translational medicine
  • Treatment Used: Intrathecal Allogeneic Mesenchymal Stem Cell Transplantation
  • Number of Patients: 2
  • Published —
This case report describes two patients with cerebral adrenoleukodystrophy that were treated using intrathecal allogeneic mesenchymal stem cell transplantation.
Latest Advance
Study
  • Condition: X-linked Adrenoleukodystrophy (ALD)
  • Journal: Beijing da xue xue bao. Yi xue ban = Journal of Peking University. Health sciences
  • Treatment Used: Haploidentical Allogenetic Hematopoietic Stem Cell Transplantation (HSCT)
  • Number of Patients: 8
  • Published —
This study explored the outcomes of haploidentical allogeneic stem cell transplantation (HSCT) for patients with X-linked adrenoleukodystrophy (ALD), a severe inherited disorder leading to rapid neurological deterioration and premature death.
Latest Advance
Study
  • Condition: Cerebral Adrenoleukodystrophy
  • Journal: Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
  • Treatment Used: Hematopoietic Stem Cell Transplantation
  • Number of Patients: 137
  • Published —
The purpose of the study was to describe the outcomes of patients with cerebral adrenoleukodystrophy who undergo hematopoietic stem cell transplantation.
Latest Advance
Study
  • Condition: Pediatric Patients with Brain Tumors
  • Journal: Human gene therapy
  • Treatment Used: MGMT(P140K) Gene Therapy
  • Number of Patients: 7
  • Published —
This study tested the safety and feasibility of MGMT(P140K) gene therapy in the treatment of pediatric patients with poor prognosis brain tumors.
Latest Advance
Study
  • Condition: Pediatric Patients with Inherited Leukodystrophies (LD)
  • Journal: Blood advances
  • Treatment Used: Cord Blood Transplantation
  • Number of Patients: 169
  • Published —
This study defined risk factors and describe the early and late outcomes of patients with globoid cell leukodystrophy, X-linked adrenoleukodystrophy, and metachromatic leukodystrophy undergoing cord blood transplantation (CBT).
Latest Advance
Study
  • Condition: X-Linked Adrenoleukodystrophy
  • Journal: Bone marrow transplantation
  • Treatment Used: Haploidentical Bone Marrow Transplant with Cyclophosphamide
  • Number of Patients: 9
  • Published —
This study tested the safety and efficacy of using a haploidentical bone marrow transplant with a post-transplant cyclophosphamide regimen to treat patients with X-linked adrenoleukodystrophy.