Clinical Trials

Clinical Trial
  • Status: Recruiting
  • Phase: Phase 2/Phase 3
  • Intervention Type: Other, Drug
  • Participants: 60
  • Start Date: September 28, 2020
Efficacy and Safety Study of Vatiquinone for the Treatment of Mitochondrial Disease Subjects With Refractory Epilepsy
Clinical Trial
  • Status: Recruiting
  • Phase: N/A
  • Intervention Type: Other
  • Participants: 380
  • Start Date: April 3, 2017
Precision Exercise Program in Children With Malignant Hemopathies Undergoing Therapy and/or Hematopoietic Stem Cell Transplantation: The Sport Therapy Project
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Clinical Trial
  • Status: Recruiting
  • Phase: Phase 1/Phase 2
  • Intervention Type: Genetic
  • Participants: 50
  • Start Date: January 2015
A Phase I/II Clinical Trial of Lentiviral Hematopoietic Stem Cell Gene Therapy for Treatment of Developed Metachromatic Leukodystrophy and Adrenoleukodystrophy
Clinical Trial
  • Status: Recruiting
  • Participants: 50
  • Start Date: January 2014
Natural History Study of Alpers Huttenlocher Syndrome
Clinical Trial
  • Status: Recruiting
  • Participants: 1000
  • Start Date: December 2010
North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
Clinical Trial
  • Status: Active, not recruiting
  • Phase: Phase 2
  • Intervention Type: Drug
  • Participants: 94
  • Start Date: February 28, 2010
Emergency Use Protocol for EPI-743 in Acutely Ill Patients With Inherited Mitochondrial Respiratory Chain Disease Within 90 Days of End-of-Life Care
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