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Clinical Trials for
CLN5 Disease
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Clinical Trials
Clinical Trials
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Clinical Trial
Status:
Not yet recruiting
Phase:
Phase 1
Intervention Type:
Genetic
Participants:
4
Start Date:
May 1, 2021
Phase 1 Intrathecal Lumbar Administration of AAV9/CLN7 for Treatment of CLN7 Disease
Clinical Trial
Status:
Not yet recruiting
Participants:
50
Start Date:
March 31, 2021
A Retrospective, Chart Review Study to Evaluate Ocular Disease Progression in Children With Late-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
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Clinical Trial
Status:
Not yet recruiting
Participants:
50
Start Date:
March 31, 2021
A Prospective, Observational Study to Evaluate Ocular Disease Progression in Children With CLN2 Batten Disease
Clinical Trial
Status:
Not yet recruiting
Phase:
Phase 2
Intervention Type:
Drug
Participants:
24
Start Date:
February 1, 2021
A Safety, Tolerability, and Efficacy Study of PLX-200 in Participants With Mild-to-Moderate Juvenile Neuronal Ceroid Lipofuscinosis (CLN3) Disease
Clinical Trial
Status:
Not yet recruiting
Participants:
195
Start Date:
February 2021
Natural History Study of Batten Disease
Clinical Trial
Status:
Recruiting
Intervention Type:
Drug, Device
Participants:
35
Start Date:
August 19, 2020
Cerliponase Alfa Observational Study
Clinical Trial
Status:
Recruiting
Phase:
N/A
Intervention Type:
Genetic
Participants:
172
Start Date:
July 1, 2020
Using Normalization Process Theory to Evaluate Providing Pediatric Palliative Care at End-of-Life as Web-Based Training Intervention for Nurses:
Clinical Trial
Status:
Recruiting
Intervention Type:
Other
Participants:
500
Start Date:
April 8, 2020
Natural History and Long Term Clinical Assessments of All Forms of Neuronal Ceroid Lipofuscinoses - Capturing Key Symptoms and Disease Progression as Part of the Independent, International NCL DEM-CHILD Patient Database
Clinical Trial
Status:
Recruiting
Intervention Type:
Genetic
Participants:
13
Start Date:
January 24, 2020
Long-Term Follow-Up of AT-GTX-501 scAAV9 Gene Transfer in Subjects With CLN6 Batten Disease
Clinical Trial
Status:
Recruiting
Participants:
5
Start Date:
November 1, 2019
Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency (Neuronal Ceroid Lipofuscinosis Type 2) Patients
Clinical Trial
Status:
Recruiting
Participants:
30
Start Date:
March 13, 2019
A Natural History and Outcome Measure Discovery Study of Variant Late Infantile Neuronal Ceroid Lipofuscinosis Type 5 (CLN5) and Variant Late Infantile Neuronal Ceroid Lipofuscinosis Type 7 (CLN7)
Clinical Trial
Status:
Recruiting
Intervention Type:
Other
Participants:
30
Start Date:
December 1, 2018
Examining Developmental Outcomes of Children Diagnosed With CLN2 Disease
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