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Clinical Trials for
Miyoshi Myopathy
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Clinical Trial
Status:
Not yet recruiting
Phase:
Phase 3
Intervention Type:
Drug
Participants:
10
Start Date:
January 1, 2021
Efficacy Confirmation Study of NPC-09
Clinical Trial
Status:
Not yet recruiting
Phase:
Phase 2
Intervention Type:
Other, Drug
Participants:
51
Start Date:
February 1, 2020
A Randomized, Double-Blind, Placebo-Controlled, Multi-Center Study to Evaluate the Efficacy of ManNAc in Subjects With GNE Myopathy
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Clinical Trial
Status:
Recruiting
Intervention Type:
Other
Participants:
430
Start Date:
March 2014
International GNE Myopathy Patient Registry (GNE001)
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