MediFind
Condition

Mucopolysaccharidosis Type 3

Active Clinical Trials

Clinical Trial
Biological
  • Status: Active, not recruiting
  • Study Type: Biological
  • Participants: 20
  • Start Date: December 23, 2019
Open-label Pilot Study of the Effects of Anakinra in Mucopolysaccharidosis (MPS) III
Clinical Trial
Drug
  • Status: Active, not recruiting
  • Study Type: Drug
  • Participants: 9
  • Start Date: January 23, 2019
An Open, Single-arm, Multicenter Extension Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients
Clinical Trial
Other
  • Status: Recruiting
  • Participants: 60
  • Start Date: November 16, 2017
A Prospective Natural History Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)
Clinical Trial
Biological
  • Status: Recruiting
  • Study Type: Biological
  • Participants: 15
  • Start Date: October 16, 2017
Phase I/II Gene Transfer Clinical Trial of rAAV9.CMV.hNAGLU for Mucopolysaccharidosis (MPS) IIIB
Clinical Trial
Biological
  • Status: Recruiting
  • Study Type: Biological
  • Participants: 22
  • Start Date: March 2016
Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH for Mucopolysaccharidosis (MPS) IIIA