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Condition
Clinical Trials for
Pelizaeus-Merzbacher Disease
Overview
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Clinical Trials
Active Clinical Trials
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Clinical Trial
Status:
Recruiting
Phase:
Phase 2/Phase 3
Intervention Type:
Other, Drug
Participants:
60
Start Date:
September 28, 2020
Efficacy and Safety Study of Vatiquinone for the Treatment of Mitochondrial Disease Subjects With Refractory Epilepsy
Clinical Trial
Status:
Recruiting
Phase:
Phase 1
Intervention Type:
Biological
Participants:
12
Start Date:
September 2014
Augmentation of Umbilical Cord Blood Transplantation for Inherited Metabolic Diseases With Intrathecal Administration of Human Umbilical Cord Blood-Derived Oligodendrocyte-Like Cells
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Clinical Trial
Status:
Recruiting
Participants:
50
Start Date:
January 2014
Natural History Study of Alpers Huttenlocher Syndrome
Clinical Trial
Status:
Recruiting
Intervention Type:
Biological, Other
Participants:
1500
Start Date:
January 11, 2012
Longitudinal Study of Neurodegenerative Disorders