An Open-label, Single Center Study Assessing Tenapanor as a Non-CFTR-mediated Treatment of CF-related Constipation in People With CF.

Status: Recruiting
Location: See location...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 3
SUMMARY

Tenapanor is the newest FDA-approved drug for IBS with constipation (IBS-C). This study seeks to understand tenapanor as a treatment for cystic fibrosis-related constipation (CFrC) in CF patients. Participants will ingest one 50 mg tablet of tenapanor, twice daily, for a 4-week treatment period. They will also complete three questionnaires, the PAC-SYM, PAC-QoL, and IBS-SSS, and daily diaries to characterize GI symptom burden and spontaneous bowel movement (SBM) frequency.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Maximum Age: 75
Healthy Volunteers: f
View:

• Having confirmed cystic fibrosis (either by sweat chloride or genetic testing)

• Meeting criteria for CFrC

• Must include 2 of the following, with or without abdominal pain for at least 3 months, with symptom onset at least 6-months prior:

⁃ Straining in at least 25% of defecations

⁃ Bristol Stool Scale 1-2 more than 25% of defecations (change in stool form)

⁃ Sensation of incomplete evacuation more than 25% of defecations

⁃ Sensation of anorectal obstruction/blockage more than 25% of defecations

⁃ Manual disimpaction/manipulation of pelvic floor to facilitate more than 25% of defecations

⁃ Fewer than 3 spontaneous bowel movements weekly (change in stool frequency)

⁃ Loose stools rarely present without the use of laxatives

• Willingness to avoid major dietary or lifestyle changes during study.

Locations
United States
Massachusetts
Massachusetts General Hospital
RECRUITING
Boston
Contact Information
Primary
Chloe Butzel, BA
cbutzel@mgh.harvard.edu
6176437088
Time Frame
Start Date: 2025-06-01
Estimated Completion Date: 2027-06-30
Participants
Target number of participants: 25
Treatments
Experimental: Cystic fibrosis patients with CF-related constipation
Related Therapeutic Areas
Sponsors
Leads: Massachusetts General Hospital
Collaborators: Ardelyx

This content was sourced from clinicaltrials.gov