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A Phase I/III Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of Intracerebral Putamen Transplantation of NouvNeu001 Injection for Multiple System Atrophy

Status: Recruiting
Location: See location...
Intervention Type: Biological
Study Type: Interventional
Study Phase: Phase 1
SUMMARY

This clinical trial is designed to evaluate the safety, tolerability and preliminary efficacy of a single injection of NouvNeu001 (Human Dopaminergic Progenitor Cells Injection) in patients with Multiple System Atrophy.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 30
Maximum Age: 70
Healthy Volunteers: f
View:

• Aged between 30 and 70 years (inclusive), regardless of gender.

• The subject understands and agrees to comply with the study procedures and voluntarily provides written informed consent.

• Diagnosed with pathologically confirmed, clinically established, or clinically probable Multiple System Atrophy (MSA) according to the 2022 MDS diagnostic criteria.

• Current treatments for core MSA symptoms are inadequately controlled.

• The duration of MSA-related motor symptoms (parkinsonism and/or cerebellar ataxia) is no more than 5 years.

• Ability to walk without human assistance, defined as being able to take at least 10 steps; the use of assistive devices (e.g., a walker or cane) is permitted.

• Life expectancy of at least 3 years.

• The subject agrees not to participate in any other clinical studies for 24 months following the investigational product administration.

Locations
Other Locations
China
Beijing Tiantan Hospital, Capital Medical University
RECRUITING
Beijing
Contact Information
Primary
Meng Cai, Ph.D
caimeng@iregene.com
0086-027-59337986
Backup
Jing Zhao, PhD
zhaojing@iregene.com
Time Frame
Start Date: 2026-01-05
Estimated Completion Date: 2031-07
Participants
Target number of participants: 9
Treatments
Experimental: NouvNeu001
During the enrollment phase for the low-dose cohort, 3 participants will be randomized to the experimental arm to receive a single administration of NouvNeu001 Injection.
No_intervention: control
During the enrollment phase for the low-dose cohort, 3 participants will be randomized to the control arm, which will not receive NouvNeu001 Injection.
Sponsors
Leads: iRegene Therapeutics Co., Ltd.

This content was sourced from clinicaltrials.gov

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