Phase 2 Study of the Efficacy and Safety of ORC-13661 for the Prevention of Drug-Induced Hearing Loss in Patients Receiving Intravenous Amikacin Therapy for Pulmonary Non-Tuberculous Mycobacterium Disease

Status: Recruiting
Location: See all (5) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

The goal of this clinical trial is to test the effectiveness of the study drug, ORC-13361, in preventing hearing loss in patients with NTM infection who are undergoing treatment with IV amikacin therapy. The main question this study aims to answer is: * Is ORC-13661 effective for preventing or lessening hearing loss induced by amikacin treatment? * Is ORC-13661 effective for preventing or lessening other measures of hearing impairment? Participants will be asked to take a study drug while they are being treated with IV amikacin. Participants will take study drug for 90 days or until the end of their amikacin treatment, whichever comes first. During this time, researchers will gather clinical data on the participants' health. Researchers will compare three groups - two groups taking different doses of the study drug and one group taking a placebo drug - to see if dose of drug has any effect on preventing hearing loss. A placebo is a look-alike substance that contains no active drug.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Maximum Age: 80
Healthy Volunteers: f
View:

• Providing informed consent, documented by signing and dating the currently valid informed consent form.

• Considered by the Investigator to have unimpaired consent capacity, without reliance on a legally authorized representative.

• Stated willingness and ability to comply with study procedures and availability for the duration of the study.

• Aged \> 18 and \< 80.

• NTM infection meeting current Pulmonary NTM guidelines from the American Thoracic Society and the Infectious Diseases Society of America (ATS/IDSA) for systemic (IV) aminoglycoside therapy.

• Anticipated duration of IV amikacin treatment of at least 30 days at time of study entry.

• Statement of ability to take oral medication and adhere to the daily dosing regimen.

• For females of reproductive potential: If they are of childbearing potential, they must agree in writing to practice an effective double barrier method of contraception from the signing of the informed consent form until 1 month following discontinuation of study drug treatment or agree to practice true abstinence, when this is consistent with the preferred and usual lifestyle of the subject.

• For males of reproductive potential: Agree to practice effective barrier contraception from the signing of the informed consent form until 3 months (one spermatogenesis cycle) following the last dose of study drug or agree to practice true abstinence.

Locations
United States
Colorado
National Jewish Health
NOT_YET_RECRUITING
Denver
Minnesota
Mayo Clinic
RECRUITING
Rochester
Oregon
Oregon Health & Science University
RECRUITING
Portland
South Carolina
Medical University of South Carolina
NOT_YET_RECRUITING
Charleston
Texas
University of Texas Health Science Center
RECRUITING
Tyler
Contact Information
Primary
Daniel Bouchat
johdanie@ohsu.edu
503-494-2568
Backup
Ted Warnock
warnockt@ohsu.edu
503-494-8121
Time Frame
Start Date: 2025-06-02
Estimated Completion Date: 2028-02-29
Participants
Target number of participants: 105
Treatments
Experimental: High Dose ORC-13661
This arm is a daily treatment regimen of study drug (ORC-13661) with a loading dose of 150mg followed by a daily dose of 30mg. Treatment regimen will run concurrently with treatment with IV amikacin. Study drug treatment will continue until treatment with IV amikacin ends or 90 days, whichever is earlier.
Experimental: Low Dose ORC-13661
This arm is a daily treatment regimen of study drug (ORC-13661) with a loading dose of 60mg capsules followed by a daily dose of 12mg capsules. Treatment regimen will run concurrently with treatment with IV amikacin. Study drug treatment will continue until treatment with IV amikacin ends or 90 days, whichever is earlier.
Placebo_comparator: Placebo
This arm is a daily treatment regimen of a placebo with a loading dose and a daily dose of placebo capsules to match the treatment arms. Placebo regimen will run concurrently with treatment with IV amikacin. Placebo regimen will continue until treatment with IV amikacin ends or 90 days, whichever is earlier.
Related Therapeutic Areas
Sponsors
Collaborators: Mayo Clinic, Medical University of South Carolina, University of Washington, National Institute on Deafness and Other Communication Disorders (NIDCD), The University of Texas Health Science Center at Tyler, National Center for Advancing Translational Sciences (NCATS), Oricula Therapeutics, National Jewish Health
Leads: Kevin Winthrop

This content was sourced from clinicaltrials.gov