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A Dose-Escalation and Expansion Study of the Safety and Efficacy of XL092 in Combination With Immuno-Oncology Agents in Subjects With Unresectable Advanced or Metastatic Solid Tumors

Status: Recruiting
Location: See all (122) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 1
SUMMARY

This is a multicenter Phase 1b, open label, dose-escalation and cohort-expansion study, evaluating the safety, tolerability, pharmacokinetics (PK), preliminary antitumor activity, and effect of biomarkers of zanzalintinib administered alone, and in combination with nivolumab (doublet), nivolumab + ipilimumab (triplet) and nivolumab + relatlimab (triplet) in participants with advanced solid tumors. In the Expansion Stage, the safety and efficacy of zanzalintinib as monotherapy and in combination therapy will be further evaluated in tumor-specific Expansion Cohorts.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Healthy Volunteers: f
View:

• Cytologically or histologically confirmed solid tumor that is unresectable, locally advanced or metastatic.

• Dose-Escalation Cohorts: Participants with a solid tumor that is unresectable or metastatic and for which life-prolonging therapies do not exist or available therapies are intolerable or no longer effective.

• Expansion Cohort 1 (ccRCC): Participants with unresectable advanced or metastatic RCC with a clear cell component who have not received prior systemic therapy.

‣ Note: Prior non-vascular endothelial growth factor (VEGF) targeted adjuvant or neoadjuvant is allowed if disease recurrence occurred 6 months after the last dose.

• Expansion Cohort 2 (ccRCC): Participants with unresectable advanced or metastatic RCC with a clear cell component.

‣ Must have radiographically progressed after a combination therapy consisting of a Programmed Cell Death Protein 1 (PD-1)/Programmed death-ligand 1 (PD-L1) targeting monoclonal antibody (mAb) with a Vascular endothelial growth factor (receptor) tyrosine kinase inhibitor (VEGFR-TKI) or a PD-1 targeting mAb with a CTLA-4 mAb as the preceding line of therapy.

⁃ Must have received no more than one prior systemic anticancer therapy for unresectable advanced or metastatic renal cell carcinoma.

• Expansion Cohort 3 (mCRPC): Men with metastatic adenocarcinoma of the prostate.

‣ Must have progressed during or after one novel hormone therapy (NHT) given for castration-sensitive locally advanced (T3 or T4) or metastatic castration-sensitive prostate cancer (CSPC), M0 CRPC, or mCRPC.

• Expansion Cohort 4 (UC, ICI-naive): Participants with histologically confirmed unresectable, locally advanced or metastatic transitional cell carcinoma of the urothelium (including the renal pelvis, ureter, urinary bladder, or urethra).

‣ Must have progressed during or after prior first-line platinum-based combination therapy, including participants who received prior neoadjuvant or adjuvant platinum-containing therapy with disease recurrence \< 12 months from the end of last therapy.

⁃ Must have received no more than 1 prior line of systemic anticancer therapy for unresectable, locally advanced or metastatic disease.

• Expansion Cohort 5 (post enfortumab vedotin \[EV\] and ICI): Participants with histologically confirmed unresectable, locally advanced or metastatic predominant urothelial carcinoma.

‣ Progressive disease following prior EV or ineligible for EV, and progression following prior PD-1/PD-L1 inhibitor or ineligible for PD-1/PD-L1 inhibitor.

⁃ Prior receipt of platinum-based therapy allowed but not required.

⁃ Prior therapy with other agents allowed but not required.

• Expansion Cohort 6 (nccRCC): Participants with unresectable advanced or metastatic nccRCC of the following subtypes: Papillary, unclassified RCC, and translocation-associated, Fumarate Hydratase (FH) deficient and Succinate Dehydrogenase (SDH) deficient. Among the eligible histologic subtypes, sarcomatoid features are allowed.

‣ No prior systemic anticancer therapy is allowed except adjuvant or neoadjuvant therapy if disease recurrence occurred at least 6 months after the last dose.

• Expansion Cohort 7 (HCC): Participants with locally advanced, or metastatic and/or unresectable HCC that is not amenable to curative treatment or locoregional therapy.

• Expansion Cohort 8 (NSCLC): Participants with Stage IV non-squamous NSCLC with positive PD-L1 expression (tumor proportion score \[TPS\] 1-49%) and without prior systemic anticancer therapy for metastatic disease.

• Expansion Cohort 9 (NSCLC): Participants with Stage IV non-squamous NSCLC who have radiologically progressed following treatment with one prior immune checkpoint inhibitor (anti-PD-1 or anti-PD-L1) for metastatic disease.

• Expansion Cohort 10 (CRC): Participants with histologically confirmed unresectable, locally advanced, or metastatic adenocarcinoma of the colon or rectum.

• Expansion Cohort 11 (HNSCC): Participant with inoperable, refractory, recurrent or metastatic HNSCC of the oral cavity, oropharynx, hypopharynx, and larynx. PD-L1 combined positive score (CPS) ≥1.

• Expansion Cohort 12 (ccRCC): Participants with unresectable advance or metastatic RCC with a clear cell component, including participants who also have a sacromatoid feature.

‣ Must have received no more than two prior lines of systemic anticancer therapy for unresectable advanced or metastatic renal cell carcinoma

• Expansion Cohort 13 and Cohort 14 (ccRCC 1L): Participants with unresectable advanced or metastatic RCC with a clear component, including participants who also have a sacromatoid feature.

• For all Expansion Cohorts except Cohort 3: Measurable disease per RECIST 1.1 as determined by the Investigator.

• For Expansion Cohorts 1 - 11 Only: Archival tumor tissue material, if available, or fresh tumor tissue if it can be safely obtained.

• Recovery to baseline or ≤ Grade 1 common terminology criteria for adverse events (CTCAE) v5 from AE(s) related to any prior treatments unless AE(s) are deemed clinically nonsignificant by the Investigator and/or stable on supportive therapy.

• Karnofsky Performance Status (KPS) ≥ 70%.

• Adequate organ and marrow function.

• Sexually active fertile participants and their partners must agree to use highly effective methods of contraception.

• Females of childbearing potential must not be pregnant at screening.

Locations
United States
Arizona
Exelixis Clinical Site #67
RECRUITING
Phoenix
Exelixis Clinical Site #1
RECRUITING
Tucson
California
Exelixis Clinical Site #123
RECRUITING
Palo Alto
Exelixis Clinical Site #59
RECRUITING
Santa Barbara
Colorado
Exelixis Clinical Site #87
RECRUITING
Littleton
Connecticut
Exelixis Clinical Site #62
RECRUITING
New Haven
Delaware
Exelixis Clinical Site #49
ACTIVE_NOT_RECRUITING
Newark
Florida
Exelixis Clinical Site #48
RECRUITING
Celebration
Exelixis Clinical Site #11
RECRUITING
Gainesville
Exelixis Clinical Site #78
RECRUITING
Jacksonville
Exelixis Clinical Site #47
RECRUITING
Miami
Exelixis Clinical Site #61
RECRUITING
Plantation
Exelixis Clinical Site #8
RECRUITING
Tampa
Illinois
Exelixis Clinical Site #26
RECRUITING
Chicago
Indiana
Exelixis Clinical Site #4
RECRUITING
Indianapolis
Kentucky
Exelixis Clinical Site #122
RECRUITING
Louisville
Massachusetts
Exelixis Clinical Site #7
RECRUITING
Boston
Maryland
Exelixis Clinical Site #14
RECRUITING
Baltimore
Michigan
Exelixis Clinical Site #13
RECRUITING
Detroit
Exelixis Clinical Site #65
RECRUITING
Detroit
Minnesota
Exelixis Clinical Site #68
RECRUITING
Rochester
North Carolina
Exelixis Clinical Site #12
RECRUITING
Durham
Nebraska
Exelixis Clinical Site #2
RECRUITING
Omaha
Exelixis Clinical Site #5
ACTIVE_NOT_RECRUITING
Omaha
New Jersey
Exelixis Clinical Site #88
RECRUITING
East Brunswick
Exelixis Clinical Site #105
RECRUITING
Hackensack
Nevada
Exelixis Clinical Site #55
RECRUITING
Las Vegas
New York
Exelixis Clinical Site #6
RECRUITING
New York
Exelixis Clinical Site #60
RECRUITING
New York
Exelixis Clinical Site #76
RECRUITING
Syracuse
Ohio
Exelixis Clinical Site #10
RECRUITING
Cleveland
Oregon
Exelixis Clinical Site #51
RECRUITING
Portland
Pennsylvania
Exelixis Clinical Site #104
RECRUITING
Hershey
Exelixis Clinical Site #98
RECRUITING
Philadelphia
Exelixis Clinical Site #24
RECRUITING
Pittsburgh
Exelixis Clinical Site #32
RECRUITING
Pittsburgh
South Carolina
Exelixis Clinical Site #9
RECRUITING
Myrtle Beach
Tennessee
Exelixis Clinical Site #3
RECRUITING
Nashville
Texas
Exelixis Clinical Site #46
RECRUITING
Austin
Exelixis Clinical Site #111
RECRUITING
Dallas
Exelixis Clinical Site #89
RECRUITING
Dallas
Exelixis Clinical Site #73
RECRUITING
Irving
Exelixis Clinical Site #50
RECRUITING
Plano
Exelixis Clinical Site #70
RECRUITING
Tyler
Virginia
Exelixis Clinical Site #66
RECRUITING
Charlottesville
Wisconsin
Exelixis Clinical Site #33
RECRUITING
Milwaukee
Other Locations
Australia
Exelixis Clinical Site #116
RECRUITING
Albury
Exelixis Clinical Site #35
RECRUITING
Birtinya
Exelixis Clinical Site #16
RECRUITING
Brisbane
Exelixis Clinical Site #42
RECRUITING
Saint Leonards
Exelixis Clinical Site #36
RECRUITING
Sydney
Austria
Exelixis Clinical Site #94
RECRUITING
Graz
Exelixis Clinical Site #31
COMPLETED
Salzburg
Exelixis Clinical Site #29
RECRUITING
Vienna
Exelixis Clinical Site #106
RECRUITING
Wein
Belgium
Exelixis Clinical Site #39
RECRUITING
Anderlecht
Exelixis Clinical Site #37
RECRUITING
Kortrijk
France
Exelixis Clinical Site #85
RECRUITING
Besançon
Exelixis Clinical Site #96
RECRUITING
Bordeaux
Exelixis Clinical Site #79
RECRUITING
Caen
Exelixis Clinical Site #118
RECRUITING
Clermont-ferrand
Exelixis Clinical Site #109
WITHDRAWN
Lyon
Exelixis Clinical Site #92
RECRUITING
Marseille
Exelixis Clinical Site #64
RECRUITING
Nice
Exelixis Clinical Site #83
RECRUITING
Paris
Exelixis Clinical Site #91
WITHDRAWN
Paris
Exelixis Clinical Site #80
RECRUITING
Rennes
Exelixis Clinical Site #63
RECRUITING
Saint-herblain
Exelixis Clinical Site #75
RECRUITING
Strasbourg
Exelixis Clinical Site #84
RECRUITING
Vandœuvre-lès-nancy
Exelixis Clinical Site #115
RECRUITING
Villejuif
Germany
Exelixis Clinical Site #103
RECRUITING
Essen
Exelixis Clinical Site #113
RECRUITING
Hamburg
Exelixis Clinical Site #108
RECRUITING
Heidelberg
Exelixis Clinical Site #82
RECRUITING
Herne
Exelixis Clinical Site #93
RECRUITING
Jena
Exelixis Clinical Site #112
COMPLETED
München
Exelixis Clinical Site #102
RECRUITING
Nürtingen
Exelixis Clinical Site #107
RECRUITING
Trier
Exelixis Clinical Site #95
RECRUITING
Tübingen
Israel
Exelixis Clinical Site #86
RECRUITING
Beersheba
Exelixis Clinical Site #72
RECRUITING
Haifa
Exelixis Clinical Site #52
RECRUITING
Jerusalem
Exelixis Clinical Site #71
RECRUITING
Petah Tikva
Exelixis Clinical Site #69
RECRUITING
Tel Aviv
Exelixis Clinical Site #38
RECRUITING
Ẕerifin
Italy
Exelixis Clinical Site #121
RECRUITING
Ancona
Exelixis Clinical Site #117
RECRUITING
Bologna
Exelixis Clinical Site #90
RECRUITING
Florence
Exelixis Clinical Site #101
RECRUITING
Milan
Exelixis Clinical Site #81
RECRUITING
Milan
Exelixis Clinical Site #40
RECRUITING
Naples
Exelixis Clinical Site #74
RECRUITING
Ravenna
New Zealand
Exelixis Clinical Site #30
RECRUITING
Grafton
Exelixis Clinical Site #45
RECRUITING
Hamilton
Poland
Exelixis Clinical Site #20
RECRUITING
Bydgoszcz
Exelixis Clinical Site #28
RECRUITING
Gdansk
Exelixis Clinical Site #34
RECRUITING
Otwock
Exelixis Clinical Site #54
RECRUITING
Poznan
Exelixis Clinical Site #114
RECRUITING
Wroclaw
Spain
Exelixis Clinical Site #41
RECRUITING
Badajoz
Exelixis Clinical Site #15
RECRUITING
Barcelona
Exelixis Clinical Site #27
RECRUITING
Barcelona
Exelixis Clinical Site #53
RECRUITING
Barcelona
Exelixis Clinical Site #120
RECRUITING
L'hospitalet De Llobregat
Exelixis Clinical Site #100
RECRUITING
Madrid
Exelixis Clinical Site #19
RECRUITING
Madrid
Exelixis Clinical Site #43
RECRUITING
Madrid
Exelixis Clinical Site #57
RECRUITING
Madrid
Exelixis Clinical Site #58
RECRUITING
Madrid
Exelixis Clinical Site #77
RECRUITING
Madrid
Exelixis Clinical Site #18
RECRUITING
Pamplona
Exelixis Clinical Site #119
RECRUITING
Santander
Exelixis Clinical Site #23
RECRUITING
Seville
Exelixis Clinical Site #25
RECRUITING
Valencia
Exelixis Clinical Site #56
RECRUITING
Valencia
Switzerland
Exelixis Clinical Site #21
COMPLETED
Chur
Exelixis Clinical Site #22
RECRUITING
Sankt Gallen
Exelixis Clinical Site #44
RECRUITING
Winterthur
United Kingdom
Exelixis Clinical Site #110
RECRUITING
Cambridge
Exelixis Clinical Site #99
RECRUITING
London
Exelixis Clinical Site #97
RECRUITING
Middlesex
Contact Information
Primary
Exelixis Clinical Trials
druginfo@exelixis.com
1-888-EXELIXIS (888-393-5494)
Backup
Backup or International
650-837-7400
Time Frame
Start Date: 2021-12-14
Estimated Completion Date: 2030-06-28
Participants
Target number of participants: 1314
Treatments
Experimental: Zanzalintinib + Nivolumab Dose-Escalation Cohorts
Approximately 12 participants will accrue across 1-2 dose levels of Zanzalintinib following the rolling 6 design.
Experimental: Zanzalintinib + Nivolumab + Ipilimumab Dose-Escalation Cohorts
Approximately 12 participants will accrue across 1-2 dose levels of Zanzalintinib following the rolling 6 design.
Experimental: Zanzalintinib + Nivolumab Expansion Cohorts
The recommended dose from the dose-escalation stage may be further explored in tumor-specific cohorts.
Experimental: Zanzalintinib + Nivolumab + Ipilimumab Expansion Cohorts
The recommended dose from the dose-escalation stage may be further explored in tumor-specific cohorts.
Experimental: Zanzalintinib Single-Agent Expansion Cohorts
Experimental: Zanzalintinib + Nivolumab + Relatlimab Dose-Escalation Cohorts
Approximately 12 participants will accrue across 1-2 dose levels of Zanzalintinib following the rolling 6 design.
Experimental: Zanzalintinib + Nivolumab + Relatlimab Expansion Cohorts
The recommended dose from the dose-escalation stage may be further explored in tumor-specific cohorts.
Sponsors
Leads: Exelixis

This content was sourced from clinicaltrials.gov

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