Medications for Methylmalonic Acidemia
These are drugs that have been approved by the US Food and Drug Administration (FDA), meaning they have been determined to be safe and effective for use in Methylmalonic Acidemia.
Found 1 Approved Drug for Methylmalonic Acidemia
Carbaglu
Generic Name
Carglumic
Carbaglu
Generic Name
Carglumic
Form: Tablet
Method of administration: Oral
FDA approval date: March 18, 2010
Classification: Carbamoyl Phosphate Synthetase 1 Activator
CARBAGLU is a carbamoyl phosphate synthetase 1 (CPS 1) activator indicated in pediatric and adult patients as: Adjunctive therapy to standard of care for the treatment of acute hyperammonemia due to N-acetylglutamate synthase (NAGS) deficiency.
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