Phase 2, Randomized, Patient- and Rater-blinded Single-site Trial Evaluating Safety and Efficacy of Efgartigimod in Patients with Guillain-Barré Syndrome.

Status: Recruiting
Location: See location...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

The goal of this clinical trial is to evaluate the safety and effectiveness of Efgartigimod in patients with Guillain-Barre syndrome (GBS). The main questions it aims to answer are: * Is Efgartigimod a safe treatment option for GBS patients? * Does treatment with Efgartigimod improve patient outcomes? In addition to standard-of-care procedures and assessments, participants will: * Undergo seven blood draws during hospitalization and in four follow-up study visits to evaluate the concentration of neurofilament light chain, a protein that is elevated in patients with Guillain-Barré syndrome. The presence of neurofilament light chain is believed to be indicative of damage to the nervous system, with higher levels resulting from greater damage. * Complete the Columbia Suicide Severity Rating Scale (C-SSRS) to monitor any suicidal ideation or behaviors during the course of the study.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Healthy Volunteers: f
View:

• Provision of signed and dated informed consent form

• Stated willingness to comply with all study procedures and availability for the duration of the study

• Male or female, aged 18 years or older

• Have a diagnosis of GBS according to the National Institute of Neurological Disorders and Stroke Diagnostic Criteria for Guillain-Barré Syndrome

• Onset of GBS-related weakness ≤14 days prior to infusion

• GBS-DS score of 3, 4, or 5

Locations
United States
Pennsylvania
Hospital of University of Pennsylvania
RECRUITING
Philadelphia
Contact Information
Primary
Kelsey Moulton
kelsey.moulton@pennmedicine.upenn.edu
267-593-9459
Time Frame
Start Date: 2024-09-10
Estimated Completion Date: 2027-05
Participants
Target number of participants: 30
Treatments
Experimental: Efgartigimod Alfa-Fcab
20mg/kg of Intravenous efgartigimod on days 1 and 5, with normal saline administered as placebo on days 2-4
Active_comparator: Intravenous Immunoglobulin (IVIg)
0.4g/kg of IVIg daily for 5 days
Sponsors
Leads: Chafic Karam
Collaborators: argenx

This content was sourced from clinicaltrials.gov