Medications for N-Acetylglutamate Synthase Deficiency
These are drugs that have been approved by the US Food and Drug Administration (FDA), meaning they have been determined to be safe and effective for use in N-Acetylglutamate Synthase Deficiency.
Found 2 Approved Drugs for N-Acetylglutamate Synthase Deficiency
Carbaglu
Generic Name
Carglumic
Carbaglu
Generic Name
Carglumic
Form: Tablet
Method of administration: Oral
FDA approval date: March 18, 2010
Classification: Carbamoyl Phosphate Synthetase 1 Activator
CARBAGLU is a carbamoyl phosphate synthetase 1 (CPS 1) activator indicated in pediatric and adult patients as: Adjunctive therapy to standard of care for the treatment of acute hyperammonemia due to N-acetylglutamate synthase (NAGS) deficiency.
Phenylbutyrate
Brand Names
Olpruva, Buphenyl, Ravicti, Pheburane
Phenylbutyrate
Brand Names
Olpruva, Buphenyl, Ravicti, Pheburane
Form: Pellet, Tablet, Kit, Powder, Liquid
Method of administration: Oral
FDA approval date: April 30, 1996
Classification: Nitrogen Binding Agent
OLPRUVA is indicated as adjunctive therapy to standard of care, which includes dietary management, for the chronic management of adult and pediatric patients weighing 20 kg or greater and with a body surface area (BSA) of.
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