A Phase III, International, Multicenter, Randomised Open Label Study to Evaluate the Efficacy and Safety of Obinutuzumab Versus MMF in Patients With Childhood Onset Idiopathic Nephrotic Syndrome

Status: Active_not_recruiting
Location: See all (55) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 3
SUMMARY

This open-label, randomized multicenter study is to assess the efficacy, safety, and pharmacokinetics (PK)/pharmacodynamics (PD) of obinutuzumab compared with mycophenolate mofetil (MMF) in children and young adults (aged \>= 2-25 years) with frequently relapsing nephrotic syndrome (FRNS) or steroid-dependent nephrotic syndrome (SDNS).

Eligibility
Participation Requirements
Sex: All
Minimum Age: 2
Maximum Age: 25
Healthy Volunteers: f
View:

• Diagnosis of frequently relapsing nephrotic syndrome (FRNS) or steroid dependent nephrotic syndrome (SDNS) before the age of 18 years

• Must be in complete remission defined by the absence of edema, UPCR \<= 0.2 g/g at screening and have three consecutive daily urine dipstick readings of trace or negative for protein within the week prior to randomization

• Must have had at least one relapse in the 6 months prior to screening, after discontinuation of or while receiving oral corticosteroids and/or immunosuppressive therapy to prevent relapses

• Participants having received cyclophosphamide in the 6 months prior to randomization must have experienced at least 1 relapse subsequent to cyclophosphamide discontinuation

• Estimated glomerular filtration rate (eGFR) within normal range for age

• For females of childbearing potential: participants who agree to remain abstinent (refrain from heterosexual intercourse) or use highly effective contraception, during the treatment period and for 18 months after the final dose of obinutuzumab and for 6 weeks after the final dose of MMF

• For males: participants who agree to remain abstinent (refrain from heterosexual intercourse) or use contraceptive methods, and agree to refrain from donating sperm during the treatment period and for 90 days after the final dose of MMF

Locations
United States
California
Cedars Sinai Medical Center
Los Angeles
Lucile Packard Children's Hospital - Stanford
Palo Alto
University of California Benioff Children's Hospital
San Francisco
Washington, D.c.
Children's National Hospital
Washington D.c.
Florida
Memorial Healthcare System
Hollywood
Nicklaus Children's Hospital
Miami
Nemours Children's Hospital
Orlando
University of South Florida
Tampa
Georgia
Children's Healthcare of Atlanta Center for Advanced Pediatrics
Atlanta
Michigan
University of Michigan
Ann Arbor
North Carolina
UNC Hospitals Outpatient Center at Eastowne
Chapel Hill
Levine Children's Hospital
Charlotte
Duke University Health Systems
Durham
New Jersey
Hackensack University Medical Center
Hackensack
Utah
University of Utah - Primary Children's Hospital - PPDS
Salt Lake City
Virginia
University of Virginia Health System
Charlottesville
Other Locations
Belgium
Hôpital Universitaire des Enfants Reine Fabiola
Brussels
UZ Gent
Ghent
Brazil
Instituto Méderi de Pesquisa e Saúde
Passo Fundo
Irmandade Da Santa Casa de Misericordia de Porto Alegre
Porto Alegre
Fundacao Faculdade Regional de Medicina de Sao Jose Do Rio Preto Hospital de Base - PPDS
São José Do Rio Preto
Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo
São Paulo
China
Peking University First Hospital
Beijing
The First Affiliated Hospital of Sun Yat-sen University
Guangzhou
The children's hospital , Zhejiang university school of medicine
Hangzhou
Tongji Hosp, Tongji Med. Col, Huazhong Univ. of Sci. & Tech
Wuhan
Xi'an Children's Hospital
Xi'an
Henan Children's Hospital Zhengzhou Children's Hospital
Zhengzhou
France
Chu Toulouse
Bron
Hopital Femme Mere Enfants
Bron
Hopital Henri Mondor
Créteil
CHU Montpellier- Hopital Arnaud de VIlleneuve
Montpellier
CHU de Nice
Nice
Hopital Necker - Enfants Malades
Paris
Hopital Robert Debre
Paris
Italy
Istituto G Gaslini Ospedale Pediatrico IRCCS - INCIPIT - PIN
Genoa
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico - Clinica De Marchi - INCIPIT - PIN
Milan
Ospedale Infantile Regina Margherita - INCIPIT - PIN
Turin
Japan
Hokkaido University Hospital
Hokkaido
Kobe University Hospital
Hyōgo
Hyogo prefectural Kobe Children's Hospital
Hyogoken
Kitasato University Hospital
Kanagawa
Yokohama City University Medical Center
Kanagawa
Dokkyo Medical University Hospital
Mibu-machi
Shiga University Of Medical Science Hospital
Shiga
National Center for Child Health and Development
Tokyo
Tokyo Metropolitan Children's Medical Center
Tokyo
Poland
Uniwersytecki Szpital Kliniczny w Bialymstoku
Bia?ystok
In-VIVO Osrodek Badan Klinicznych
Bydgoszcz
Uniwersyteckie Centrum Kliniczne
Gdansk
Dzieciecy Szpital Kliniczny UCK WUM
Warsaw
Spain
Hospital Universitario Cruces
Barakaldo
Hospital Sant Joan de Deu - PIN
Barcelona
Hospital Universitario Marques de Valdecilla
Santander
Turkey
Celal Bayar University Medical Faculty
Manisa
Time Frame
Start Date: 2023-03-29
Completion Date: 2026-09-04
Participants
Target number of participants: 85
Treatments
Experimental: Obinutuzumab (Group A)
Participants in Group A will receive obinutuzumab 1000 milligrams (mg) (or 20 mg/ kilogram \[kg\] for participants \<45 kg) administered by intravenous (IV) infusion on Days 1, 15, 168 (Week 24), and 182 (Week 26).
Active_comparator: MMF (Group B)
Participants in Group B will receive oral MMF 600 mg/m\^2 twice a day (BID) (target 1200 mg/m2/day in divided doses, maximum 2 g/day) to Week 52.
Related Therapeutic Areas
Sponsors
Leads: Hoffmann-La Roche

This content was sourced from clinicaltrials.gov