A Phase 1/1b Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Immunogenicity of Single and Multiple Ascending Doses of BCX17725 in Healthy Participants and Multiple Doses of BCX17725 in Participants With Netherton Syndrome

Status: Recruiting
Location: See all (2) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 1
SUMMARY

This is a first-in-human, Phase 1/1b, 3-part study that includes the evaluation of safety, tolerability, pharmacokinetics (PK), and immunogenicity of BCX17725 when administered via single and multiple doses in healthy adult participants (Parts 1 and 2), and multiple doses in participants with Netherton Syndrome (Part 3).

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Maximum Age: 65
Healthy Volunteers: t
View:

• Male or non-pregnant, non-lactating female aged 18 to 55 years, inclusive (Parts 1 and 2) or aged 18 to 65 years, inclusive (Part 3)

• Confirmed diagnosis of Netherton syndrome (Part 3 only)

• BMI between 18 and 30 kg/m\^2, inclusive (Parts 1 and 2 only)

• Estimated glomerular filtration rate (eGFR) of ≥ 90 mL/min/1.73 m\^2 (Parts 1 and 2) or ≥ 60 mL/min/1.73 m\^2 (Part 3)

• Agree to follow the protocol contraception requirements from screening until 90 days after the last dose of study drug

• In the opinion of the investigator, expected to adequately comply with all required study procedures and restrictions for the duration of the study

Locations
United States
Indiana
Investigative site
RECRUITING
Indianapolis
Other Locations
Australia
Investigative site
RECRUITING
Brisbane
Contact Information
Primary
BioCryst Pharmaceuticals, Inc.
clinicaltrials@biocryst.com
+1 919 859 1302
Time Frame
Start Date: 2024-09-26
Estimated Completion Date: 2026-03
Participants
Target number of participants: 66
Treatments
Experimental: Part 1 - BCX17725 single dose
Participants randomized to BCX17725 will receive BCX17725 as a single dose in sequential ascending dose cohorts
Experimental: Part 1 - placebo single dose
Participants randomized to placebo will receive placebo as a single dose
Experimental: Part 2 - BCX17725 multiple doses
Participants randomized to BCX17725 will receive BCX17725 as multiple doses in sequential ascending dose cohorts
Experimental: Part 2 - placebo multiple doses
Participants randomized to placebo will receive placebo as multiple doses
Experimental: Part 3 - BCX17725 multiple doses
Participants will receive BCX17725 as multiple doses
Related Therapeutic Areas
Sponsors
Leads: BioCryst Pharmaceuticals

This content was sourced from clinicaltrials.gov