A Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and Breastfeeding

Status: Recruiting
Location: See all (3) locations...
Intervention Type: Drug
Study Type: Observational
SUMMARY

This is a Phase 4 observational study designed to assess the impact of Palynziq ® (pegvaliase) treatment in pregnant women with PKU and on their offspring who were exposed to pegvaliase at any time during pregnancy and breastfeeding.

Eligibility
Participation Requirements
Sex: Female
View:

• Subject (or a legally authorized representative) consent obtained prior to enrollment. Consent will be obtained in compliance with any country-specific regulations or requirements

• Confirmation of ongoing pregnancy. Subjects with unknown outcomes will be classified as prospective pregnancies; subjects who have undergone prenatal testing (eg, targeted ultrasound, amniocentesis) regardless of findings will be classified as retrospective pregnancies

• Diagnosed with PKU per local standard of care

• Documentation that the subject was treated with pegvaliase at any point starting from 2 weeks prior to the date of LMP

• Agrees to permit the Investigator (ie, CRP, CCA, PI) to contact the subject's HCPs (eg, PCP, PKU-treating physician, OB, nurse, midwife) and the infant's HCP (eg, pediatrician, neonatologist) for medical information

Locations
United States
North Carolina
Syneos Health
RECRUITING
Wilmington
Other Locations
Germany
Universitaetsklinikum Hamburg Eppendorf
NOT_YET_RECRUITING
Hamburg
Italy
Ospedale San Paolo
NOT_YET_RECRUITING
Milan
Contact Information
Primary
165-504 Program Director
medinfo@bmrn.com
1-800-983-4587
Time Frame
Start Date: 2022-11-22
Estimated Completion Date: 2032-10-04
Participants
Target number of participants: 50
Treatments
Pregnant Women with PKU
This study will enroll pregnant women diagnosed with PKU who have been treated with pegvaliase from 2 weeks prior to LMP or at any time during pregnancy.
Sponsors
Collaborators: Syneos Health
Leads: BioMarin Pharmaceutical

This content was sourced from clinicaltrials.gov