A Phase 1b/2 Study of AZD0120 (Also Known as GC012F), a Chimeric Antigen Receptor T Cell Therapy Targeting CD19 and B Cell Maturation Antigen in Participants With Relapsed or Refractory AL Amyloidosis.

Status: Recruiting
Location: See all (15) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 1/Phase 2
SUMMARY

Open-label Phase 1b/2 study with primary objective of this study is to evaluate the safety, tolerability and efficacy of AZD0120 in participants with light chain (AL) amyloidosis.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Healthy Volunteers: f
View:

• Confirmed histopathological diagnosis of AL amyloidosis

• One or more organs currently or historically impacted by AL amyloidosis according to consensus guidelines

• Measurable hematologic disease: dFLC \> 20 mg/L or serum M-protein \> 5g/L

• Relapsed disease or refractory disease defined as a need for additional therapy after at least 1 line of anti-plasma cell-directed therapy.

• ECOG performance status of 0 to 1

• Must be able and willing to adhere to the study visit schedule and other protocol requirements

• Women of child-bearing potential (WCBP) must have a negative serum pregnancy test prior to treatment. All sexually active WCBP and all sexually active male subjects must agree to use effective methods of birth control throughout the study.

Locations
United States
Arizona
Research Site
NOT_YET_RECRUITING
Phoenix
California
Research Site
NOT_YET_RECRUITING
San Francisco
Florida
Research Site
RECRUITING
Tampa
Massachusetts
Research Site
NOT_YET_RECRUITING
Boston
Michigan
Research Site
RECRUITING
Detroit
Minnesota
Research Site
NOT_YET_RECRUITING
Rochester
Missouri
Research Site
RECRUITING
St Louis
New York
Research Site
RECRUITING
New York
Research Site
RECRUITING
New York
Research Site
RECRUITING
New York
Ohio
Research Site
NOT_YET_RECRUITING
Cleveland
Tennessee
Research Site
NOT_YET_RECRUITING
Nashville
Other Locations
Canada
Research Site
NOT_YET_RECRUITING
Calgary
Research Site
NOT_YET_RECRUITING
Toronto
United Kingdom
Research Site
NOT_YET_RECRUITING
London
Contact Information
Primary
Alexion Pharmaceuticals, Inc. (Sponsor)
clinicaltrials@alexion.com
1-855-752-2356
Time Frame
Start Date: 2025-08-18
Estimated Completion Date: 2030-12-19
Participants
Target number of participants: 91
Treatments
Experimental: AZD0120
Participants will receive weight-based dose of AZD0120.
Related Therapeutic Areas
Sponsors
Leads: Alexion Pharmaceuticals, Inc.

This content was sourced from clinicaltrials.gov