Precision Administration of Anti-thymocyte Globulin With or Without Verapamil in Adolescents and Young Adults With Type 1 Diabetes

Status: Recruiting
Location: See all (2) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

T cell directed therapy, anti-thymocyte globulin (ATG), in low doses, has been shown to lower HbA1c and preserve endogenous insulin production (measured by C-peptide) in individuals with recently diagnosed type 1 diabetes (T1D). However, not all individuals who received ATG responded to the therapy (i.e., non-responders). Additionally, use of ATG alone does not address inherent beta cell stress. A calcium channel blocker, verapamil, has demonstrated C-peptide preservation in newly diagnosed T1D. Investigators will identify those mostly likely to respond to ATG using an ex vivo predictive biomarker of response to ATG. In addition, Investigators will use sequential therapies to increase efficacy (ATG followed by verapamil) and explore synergistic mechanisms. This will be assessing with in depth immunophenotyping and quantify biomarkers of beta cell stress, cell death, and abnormal prohormone processing. Finally, novel clinical trial endpoints will be assessed for their ability to predict treatment efficacy earlier than the standard endpoint at 1 year.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 6
Maximum Age: 35
Healthy Volunteers: f
View:

• Must be \>= 6 years \<= 35

• Must have a diagnosis of T1D for less than 100 days at randomization

• Willing to provide Informed Consent or have a parent or legal guardian provide informed consent if the subject is \<18 years of age

• Positive for at least one islet cell autoantibody; GAD65A, mIAA, if obtained within 10 days of the onset of insulin therapy, IA-2A, ICA, or ZnT8A

• Must have stimulated C-peptide levels of 0.2 pmol/ml measured during a mixed meal tolerance test (MMTT) conducted at least 21 days from diagnosis of diabetes. Randomization should occur within one month (37 days) of the MMTT.

• Subjects who are EBV seronegative at screening must be EBV PCR negative within 30 days of randomization and may not have had signs or symptoms of an EBV compatible illness lasting longer than 7 days within 30 days of randomization

• Be at least 6 weeks from last live immunization

• Participants are required to receive killed influenza vaccination at least 2 weeks prior to randomization when vaccine for the current or upcoming flu season is available

• Be willing to forgo live vaccines during the treatment period and for 3 months following last dose of study drug

⁃ Be willing to comply with intensive diabetes management

Locations
United States
Colorado
Barbara Davis Center for Diabetes
RECRUITING
Aurora
Florida
University of Florida
RECRUITING
Gainesville
Contact Information
Primary
Jennifer L Hosford, MPH
jennifer.hosford@peds.ufl.edu
352-294-5760
Time Frame
Start Date: 2025-11-12
Estimated Completion Date: 2030-08
Participants
Target number of participants: 60
Treatments
Experimental: Anti-thymocyte globulin (ATG) intravenous infusion
ATG (brand name Thymoglobulin) a polyclonal T cell antibody preparation. It will be given at low doses (0.5 mg/kg Day 1 then 2 mg/kg Day 2).
Placebo_comparator: Placebo-ATG
Saline placebo
Experimental: verapamil extended release capsule
Open label administration at 120, 240 or 360 mg daily based on weight and ECG findings
Related Therapeutic Areas
Sponsors
Collaborators: University of Miami, University of Colorado, Denver
Leads: University of Florida

This content was sourced from clinicaltrials.gov