An Open-label, Single-arm Study Evaluating the Activity, Safety, and Pharmacokinetics of Rozanolixizumab in Pediatric Study Participants With Moderate to Severe Generalized Myasthenia Gravis

Status: Recruiting
Location: See all (11) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 2/Phase 3
SUMMARY

The purpose of the study is to assess the safety and tolerability of subcutaneous (sc) administration of rozanolixizumab in pediatric participants aged ≥2 to \<18 years with generalized Myasthenia Gravis (gMG).

Eligibility
Participation Requirements
Sex: All
Minimum Age: 2
Maximum Age: 17
Healthy Volunteers: f
View:

• Study participant must be ≥2 to \<18 years of age inclusive, at the time of signing the informed consent/assent according to local regulation

• Study participant must have a documented diagnosis of generalized Myasthenia Gravis (gMG) at Screening that includes a record confirming the presence of MG specific autoantibodies to acetylcholine receptor (AChR) or muscle-specific kinase (MuSK) prior to Screening

• Study participant has Myasthenia Gravis Foundation of America (MGFA) Clinical Classification II to IVa at Screening

• Study participant has received existing conventional treatment(s) for gMG (eg, pyridostigmine, corticosteroids, and/or immune suppressants) prior to Screening

• Study participant has had an unsatisfactory clinical response or worsening of gMG symptoms and is in need of additional therapy (for example, plasma exchange (PEX) or treatment with intravenous immunoglobulin (IVIg))

Locations
United States
Texas
Mg0006 50574
WITHDRAWN
Denton
Other Locations
Italy
Mg0006 40290
RECRUITING
Bologna
Mg0006 40144
RECRUITING
Milan
Mg0006 40733
RECRUITING
Napoli
Japan
Mg0006 20340
RECRUITING
Fuchu-shi
Mg0006 20339
RECRUITING
Ōbu
Mg0006 20343
RECRUITING
Sagamihara
Poland
Mg0006 40734
RECRUITING
Lodz
Mg0006 40155
RECRUITING
Warsaw
Taiwan
Mg0006 20081
RECRUITING
Taipei
Mg0006 20095
RECRUITING
Taipei
Contact Information
Primary
UCB Cares
ucbcares@ucb.com
1-844-599-2273
Backup
UCB Cares
ucbcares@ucb.com
001 844 599 2273
Time Frame
Start Date: 2024-06-14
Estimated Completion Date: 2026-08-17
Participants
Target number of participants: 12
Treatments
Experimental: rozanolixizumab
Study participants will receive pre-defined doses of rozanolixizumab for 6 weeks.
Related Therapeutic Areas
Sponsors
Leads: UCB Biopharma SRL

This content was sourced from clinicaltrials.gov