Ahad A. Rahim

London, ENG WC1E6BT, United Kingdom

Last Updated: 09/26/2026

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Found 64 publications

Backbone-Minimised Nanoplasmid DNA Systems Enable High-Titre AAV Production in Suspension HEK293 Platforms.

Backbone-Minimised Nanoplasmid DNA Systems Enable High-Titre AAV Production in Suspension HEK293 Platforms.

Journal: Pharmaceutics
Published: May 13, 2026

Brain-Directed AAV Gene Therapy Rescues a Mouse Model of the CLN5 Form of Neuronal Ceroid Lipofuscinosis Disease and Normalizes a Blood Plasma Biomarker of Neurodegeneration.

Brain-Directed AAV Gene Therapy Rescues a Mouse Model of the CLN5 Form of Neuronal Ceroid Lipofuscinosis Disease and Normalizes a Blood Plasma Biomarker of Neurodegeneration.

Journal: Human gene therapy
Published: December 29, 2025

MDFIC2 is a PIEZO channel modulator that can alleviate mechanical allodynia associated with neuropathic pain.

MDFIC2 is a PIEZO channel modulator that can alleviate mechanical allodynia associated with neuropathic pain.

Journal: Proceedings of the National Academy of Sciences of the United States of America
Published: November 07, 2025

CLN7 protein functions at the interface between endolysosomes and stress granules to promote cell survival.

CLN7 protein functions at the interface between endolysosomes and stress granules to promote cell survival.

Journal: Cell death & disease
Published: April 24, 2025

Generation and Treatment of a Novel Severe Model of Visceral Gaucher Disease by Genetic Therapy.

Generation and Treatment of a Novel Severe Model of Visceral Gaucher Disease by Genetic Therapy.

Journal: Pharmaceutics
Published: March 26, 2025

In-situ hyaluronic acid-tyramine hydrogels prolong the release of extracellular vesicles and enhance stability.

In-situ hyaluronic acid-tyramine hydrogels prolong the release of extracellular vesicles and enhance stability.

Journal: International journal of pharmaceutics
Published: March 13, 2025

Genetic therapies for movement disorders - current status.

Genetic therapies for movement disorders - current status.

Journal: Journal of neurology
Published: January 02, 2025

Genetic therapies for neurological diseases.

Genetic therapies for neurological diseases.

Journal: Pharmacological reviews
Published: July 31, 2024

Comparison of different promoters to improve AAV vector-mediated gene therapy for neuronopathic Gaucher disease.

Comparison of different promoters to improve AAV vector-mediated gene therapy for neuronopathic Gaucher disease.

Journal: Human molecular genetics
Published: April 01, 2024

The relation of mTOR with diabetic complications and insulin resistance in patients with type 2 diabetes mellitus.

The relation of mTOR with diabetic complications and insulin resistance in patients with type 2 diabetes mellitus.

Journal: Diabetology & metabolic syndrome
Published: March 18, 2024

Engineering an Autonucleolytic Mammalian Suspension Host Cell Line to Reduce DNA Impurity Levels in Serum-Free Lentiviral Process Streams.

Engineering an Autonucleolytic Mammalian Suspension Host Cell Line to Reduce DNA Impurity Levels in Serum-Free Lentiviral Process Streams.

Journal: ACS synthetic biology
Published: January 24, 2024

Dual-targeting CRISPR-CasRx reduces C9orf72 ALS/FTD sense and antisense repeat RNAs in vitro and in vivo.

Dual-targeting CRISPR-CasRx reduces C9orf72 ALS/FTD sense and antisense repeat RNAs in vitro and in vivo.

Journal: Nature communications
Published: January 23, 2024
Showing 1-12 of 64

Last Updated: 09/26/2026