Last Updated: 09/26/2026
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Found 67 publications
Correction of Ineffective Erythropoiesis and Normalization of Iron Homeostasis After Exagamglogene Autotemcel in Transfusion-Dependent β-Thalassemia.
Journal: American journal of hematology
Published: May 14, 2026
Begelomab (BEGESAND®) Salvages Steroid-Resistant Acute GVHD in Pediatric Patients.
Journal: Journal of clinical medicine
Published: April 19, 2026
Barriers and opportunities to improve fluid balance recognition and reduction: a qualitative study.
Journal: Frontiers in pediatrics
Published: March 13, 2026
Clinical outcomes of lentiviral vector gene therapy for sickle cell disease.
Journal: Blood advances
Published: February 02, 2026
A prelimbic molecular clock of protein synthesis for memory persistence.
Journal: bioRxiv : the preprint server for biology
Published: January 09, 2026
Improved outcome of HSCT in STAT1 gain-of-function disease following JAK inhibition bridging.
Journal: Journal of human immunity
Published: October 27, 2025
Newborn screening reduces survival disparities in SCID after stem cell transplant: A PIDTC report.
Journal: Journal of human immunity
Published: October 27, 2025
Neurodevelopmental outcomes following hematopoietic cell transplantation for patients with severe combined immunodeficiency (SCID): A PIDTC study.
Journal: Journal of human immunity
Published: July 23, 2025
Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report.
Journal: Blood advances
Published: July 02, 2025
Hematopoietic Cell Transplantation for Wiskott-Aldrich syndrome: A PIDTC Report.
Journal: Blood advances
Published: July 02, 2025
Characterizing the Safety and Efficacy of Propofol in Critically Ill Pediatric Patients.
Journal: The journal of pediatric pharmacology and therapeutics : JPPT : the official journal of PPAG
Published: May 21, 2025
Last Updated: 09/26/2026