Last Updated: 09/26/2026
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Found 3 publications
Gene therapy for aromatic L-amino acid decarboxylase deficiency by MR-guided direct delivery of AAV2-AADC to midbrain dopaminergic neurons.
Journal: Nature communications
Published: September 07, 2020
Phenotypic characteristics of early Wolfram syndrome.
Journal: Orphanet journal of rare diseases
Published: February 13, 2013
Reliability and validity of the Wolfram Unified Rating Scale (WURS).
Journal: Orphanet journal of rare diseases
Published: June 12, 2012
Showing 1-3 of 3
Last Updated: 09/26/2026