Last Updated: 09/26/2026
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Found 63 publications
Perimacular Atrophy Following Voretigene Neparvovec-Rzyl Treatment in the Setting of Previous Contralateral Eye Treatment With a Different Viral Vector.
Journal: Translational vision science & technology
Published: June 18, 2024
Subretinal Gene Therapy Drug AGTC-501 for XLRP Phase 1/2 Multicenter Study (HORIZON): 24-Month Safety and Efficacy Results.
Journal: American journal of ophthalmology
Published: May 30, 2024
Gene Editing for CEP290-Associated Retinal Degeneration.
Journal: The New England journal of medicine
Published: May 06, 2024
Partial rescue of the full-field electroretinogram in patients with RPE65-related retinal dystrophy following gene augmentation therapy with voretigene neparvovec-rzyl.
Journal: Documenta ophthalmologica. Advances in ophthalmology
Published: March 16, 2024
Thiophene-based lipids for mRNA delivery to pulmonary and retinal tissues.
Journal: Proceedings of the National Academy of Sciences of the United States of America
Published: March 04, 2024
Preformed Vesicle Approach to LNP Manufacturing Enhances Retinal mRNA Delivery.
Journal: Small (Weinheim an der Bergstrasse, Germany)
Published: February 01, 2024
Safety and efficacy of ATSN-101 in patients with Leber congenital amaurosis caused by biallelic mutations in GUCY2D: a phase 1/2, multicentre, open-label, unilateral dose escalation study.
Journal: Lancet (London, England)
Published: December 20, 2023
The retina-brain axis and diabetic retinopathy.
Journal: European journal of ophthalmology
Published: June 01, 2023
Improved Rod Sensitivity as Assessed by Two-Color Dark-Adapted Perimetry in Patients With RPE65-Related Retinopathy Treated With Voretigene Neparvovec-rzyl.
Journal: Translational vision science & technology
Published: April 14, 2023
Development of a translatable gene augmentation therapy for CNGB1-retinitis pigmentosa.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: January 19, 2023
Peptide-guided lipid nanoparticles deliver mRNA to the neural retina of rodents and nonhuman primates.
Journal: Science advances
Published: January 11, 2023
Iatrogenic choroidal neovascularization associated with subretinal gene therapy surgery.
Journal: American journal of ophthalmology case reports
Published: March 07, 2022
Last Updated: 09/26/2026