Last Updated: 09/26/2026
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Found 8 publications
Phase 3 Randomized Trial Results of DTX401 AAV Gene Therapy for the Treatment of GSDIa.
Journal: Journal of inherited metabolic disease
Published: April 29, 2026
In vivo characterization of glycogen storage disease type III in a mouse model using glycoNOE MRI.
Journal: Magnetic resonance in medicine
Published: June 30, 2023
Glycogen storage disease type III: a mixed-methods study to assess the burden of disease.
Journal: Therapeutic advances in endocrinology and metabolism
Published: June 14, 2023
Efficacy, safety, and pharmacokinetics of teduglutide in adult Japanese patients with short bowel syndrome and intestinal failure: two phase III studies with an extension.
Journal: Surgery today
Published: February 04, 2022
Safety Findings in Pediatric Patients During Long-Term Treatment With Teduglutide for Short-Bowel Syndrome-Associated Intestinal Failure: Pooled Analysis of 4 Clinical Studies.
Journal: JPEN. Journal of parenteral and enteral nutrition
Published: September 11, 2020
Safety and Efficacy of Teduglutide in Pediatric Patients With Intestinal Failure due to Short Bowel Syndrome: A 24-Week, Phase III Study.
Journal: JPEN. Journal of parenteral and enteral nutrition
Published: March 20, 2019
Assessing the therapeutic potential of lab-made hepatocytes.
Journal: Hepatology (Baltimore, Md.)
Published: August 18, 2015
Showing 1-8 of 8
Last Updated: 09/26/2026