Last Updated: 09/26/2026
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Found 47 publications
In vivo chimeric antigen receptor (CAR)-T cell therapy.
Journal: Nature reviews. Drug discovery
Published: August 13, 2025
Preclinical proof of concept for VivoVec, a lentiviral-based platform for in vivo CAR T-cell engineering.
Journal: Journal for immunotherapy of cancer
Published: February 27, 2023
A chemically inducible IL-2 receptor signaling complex allows for effective in vitro and in vivo selection of engineered CD4+ T cells.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: November 02, 2022
Improved CRISPR genome editing using small highly active and specific engineered RNA-guided nucleases.
Journal: Nature communications
Published: January 15, 2021
Gene editing to induce FOXP3 expression in human CD4+ T cells leads to a stable regulatory phenotype and function.
Journal: Science translational medicine
Published: July 05, 2019
In Vivo Outcome of Homology-Directed Repair at the HBB Gene in HSC Using Alternative Donor Template Delivery Methods.
Journal: Molecular therapy. Nucleic acids
Published: May 29, 2019
Therapeutically relevant engraftment of a CRISPR-Cas9-edited HSC-enriched population with HbF reactivation in nonhuman primates.
Journal: Science translational medicine
Published: December 26, 2018
TALEN-Mediated Gene Editing of HBG in Human Hematopoietic Stem Cells Leads to Therapeutic Fetal Hemoglobin Induction.
Journal: Molecular therapy. Methods & clinical development
Published: September 27, 2018
Therapeutic Gene Editing Safety and Specificity.
Journal: Hematology/oncology clinics of North America
Published: September 13, 2017
Last Updated: 09/26/2026