Andrew Mcfadyen
Toronto, ON, Canada
Last Updated: 09/26/2026
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Found 9 publications
A conceptual model and practical guidance for the development, administration, and evaluation of individualized therapies.
Journal: Frontiers in medicine
Published: September 09, 2024
Ethical challenges and opportunities in the development and approval of novel therapeutics for rare diseases.
Journal: The journal of medicine access
Published: January 25, 2023
Somatic Gene Therapy Research in Pediatric Populations: Ethical Issues and Guidance for Operationalizing Early Phase Trials.
Journal: Pharmaceutical medicine
Published: November 01, 2022
Fetal Therapies and Clinical Research: Beyond Risk and Benefit.
Journal: The American journal of bioethics : AJOB
Published: March 01, 2022
Gene therapy companies have an ethical obligation to develop expanded access policies.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: March 14, 2021
Preapproval Nontrial Access and Off-Label Use: Do They Meet Criteria for Dual-Deviation Review?
Journal: The American journal of bioethics : AJOB
Published: May 29, 2019
What compassionate use means for gene therapies.
Journal: Nature biotechnology
Published: April 04, 2019
Recommendations for the management of MPS VI: systematic evidence- and consensus-based guidance.
Journal: Orphanet journal of rare diseases
Published: January 02, 2019
Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance.
Journal: Orphanet journal of rare diseases
Published: December 10, 2018
Showing 1-9 of 9
Last Updated: 09/26/2026