Annamaria Aprile
Milan, Italy
Last Updated: 09/26/2026
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Found 12 publications
Gene therapy for hemoglobinopathies: Clinical trial results and biology of hematopoietic stem cell and the bone marrow niche.
Journal: Cell reports. Medicine
Published: June 10, 2025
Inhibition of FGF23 is a therapeutic strategy to target hematopoietic stem cell niche defects in β-thalassemia.
Journal: Science translational medicine
Published: May 31, 2023
Genetic engineering meets hematopoietic stem cell biology for next-generation gene therapy.
Journal: Cell stem cell
Published: February 01, 2023
Targeting the Hematopoietic Stem Cell Niche in β-Thalassemia and Sickle Cell Disease.
Journal: Pharmaceuticals (Basel, Switzerland)
Published: March 30, 2022
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia.
Journal: Nature medicine
Published: July 25, 2018
Bone marrow stromal cells from β-thalassemia patients have impaired hematopoietic supportive capacity.
Journal: The Journal of clinical investigation
Published: June 26, 2018
Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia.
Journal: Molecular therapy. Methods & clinical development
Published: June 18, 2018
Plerixafor and G-CSF combination mobilizes hematopoietic stem and progenitors cells with a distinct transcriptional profile and a reduced in vivo homing capacity compared to plerixafor alone.
Journal: Haematologica
Published: December 31, 2016
When diagnostics meets translational research: detection of hemoglobin fractions in cellular lysates from in vitro erythroid cultures by Capillarys 2 Flex Piercing analyzer (Sebia).
Journal: Translational research : the journal of laboratory and clinical medicine
Published: June 30, 2015
Showing 1-12 of 12
Last Updated: 09/26/2026