Annarita Miccio
Paris, 75015, France
Last Updated: 09/26/2026
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Found 71 publications
Base editing of β0-thalassemia mutations as a therapeutic strategy for severe β-hemoglobinopathies.
Journal: Science translational medicine
Published: November 26, 2025
Enhanced γ-globin reactivation and sickle cell correction through a repressor-to-activator motif switch in the HBG1/2 promoters.
Journal: Molecular therapy. Nucleic acids
Published: October 08, 2025
CleanFinder: a scalable framework for comprehensive genome editing analysis.
Journal: Trends in biotechnology
Published: September 08, 2025
Multiplex base editing of BCL11A regulatory elements to treat sickle cell disease.
Journal: Cell reports. Medicine
Published: May 15, 2025
Advanced delivery systems for gene editing: A comprehensive review from the GenE-HumDi COST Action Working Group.
Journal: Molecular therapy. Nucleic acids
Published: February 24, 2025
Clinical application of base editing for treating β-thalassaemia.
Journal: Nature
Published: February 17, 2025
A CRISPR/Cas approach to β-haemoglobinopathies
Journal: Medecine sciences : M/S
Published: January 31, 2025
Dissecting the epigenetic regulation of the fetal hemoglobin genes to unravel a novel therapeutic approach for β-hemoglobinopathies.
Journal: Nucleic acids research
Published: January 10, 2025
Advancing the Integration of 'Basic/Fundamental' and Translational Cellular and Gene Therapy Science within the EBMT: Accelerating the Pathway to Progress.
Journal: Bone marrow transplantation
Published: December 10, 2024
Last Updated: 09/26/2026