Asma M. Naseem
Great Ormond Street Institute Of Child Health
London, ENG WC1N1DZ, United Kingdom
London, ENG WC1N1DZ, United Kingdom
Last Updated: 09/26/2026
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Found 24 publications
DNA-PKcs inhibitor AZD7648 reveals sgRNA cross-contaminants and enhanced sensitivity of genome engineering off-target activity in HSPCs.
Journal: Nucleic acids research
Published: December 18, 2025
In-depth characterization of stem cell potency and genotoxicity for clinical-scale ex vivo CRISPR-Cas9 gene editing.
Journal: Molecular therapy. Advances
Published: August 01, 2025
Advanced delivery systems for gene editing: A comprehensive review from the GenE-HumDi COST Action Working Group.
Journal: Molecular therapy. Nucleic acids
Published: February 24, 2025
The predisposing factors to having a coded diagnosis of Long COVID.
Journal: Public health
Published: November 29, 2024
It's all about location: Targeting the right spot for Wiskott-Aldrich syndrome.
Journal: Molecular therapy. Methods & clinical development
Published: April 29, 2024
CRISPR/Cas9-Based Disease Modeling and Functional Correction of Interleukin 7 Receptor Alpha Severe Combined Immunodeficiency in T-Lymphocytes and Hematopoietic Stem Cells.
Journal: Human gene therapy
Published: January 22, 2024
Multidimensional Response Surface Methodology for the Development of a Gene Editing Protocol for p67phox-Deficient Chronic Granulomatous Disease.
Journal: Human gene therapy
Published: December 08, 2023
Hematopoietic stem cell gene editing rescues B-cell development in X-linked agammaglobulinemia.
Journal: The Journal of allergy and clinical immunology
Published: December 01, 2023
Correction to: Sars-Cov-2 Infection in People with Type 1 Diabetes and Hospital Admission: An Analysis of Risk Factors for England.
Journal: Diabetes therapy : research, treatment and education of diabetes and related disorders
Published: October 05, 2023
SARS-CoV-2 Syncytium under the Radar: Molecular Insights of the Spike-Induced Syncytia and Potential Strategies to Limit SARS-CoV-2 Replication.
Journal: Journal of clinical medicine
Published: August 04, 2023
Sars-Cov-2 Infection in People with Type 1 Diabetes and Hospital Admission: An Analysis of Risk Factors for England.
Journal: Diabetes therapy : research, treatment and education of diabetes and related disorders
Published: May 14, 2023
An improved medium formulation for efficient ex vivo gene editing, expansion and engraftment of hematopoietic stem and progenitor cells.
Journal: Molecular therapy. Methods & clinical development
Published: August 25, 2022
Last Updated: 09/26/2026