Aurelien Jacob
Milan, 20132, Italy
Last Updated: 09/26/2026
Save publications for later
Sign Up
Not sure about your diagnosis?
Check Your Symptoms
Found 12 publications
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency.
Journal: Science translational medicine
Published: February 07, 2024
Scalable GMP-compliant gene correction of CD4+ T cells with IDLV template functionally validated in vitro and in vivo.
Journal: Molecular therapy. Methods & clinical development
Published: May 25, 2023
Unbiased assessment of genome integrity and purging of adverse outcomes at the target locus upon editing of CD4+ T-cells for the treatment of Hyper IgM1.
Journal: The EMBO journal
Published: April 04, 2023
Mobilization-based chemotherapy-free engraftment of gene-edited human hematopoietic stem cells.
Journal: Cell
Published: December 16, 2021
Monobac System-A Single Baculovirus for the Production of rAAV.
Journal: Microorganisms
Published: July 07, 2021
Gene Editing of Hematopoietic Stem Cells: Hopes and Hurdles Toward Clinical Translation.
Journal: Frontiers in genome editing
Published: October 16, 2020
Homologous Recombination Offers Advantages over Transposition-Based Systems to Generate Recombinant Baculovirus for Adeno-Associated Viral Vector Production.
Journal: Biotechnology journal
Published: May 14, 2020
Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking.
Journal: Nature biotechnology
Published: December 06, 2019
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1.
Journal: Science translational medicine
Published: March 01, 2017
Showing 1-12 of 12
Last Updated: 09/26/2026