Bella Madan
Guy's And St Thomas' NHS Foundation Trust
London, ENG, United Kingdom
London, ENG, United Kingdom
Last Updated: 09/26/2026
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Found 16 publications
Final Analysis of the Phase 1/2 Trial of Valoctocogene Roxaparvovec for Severe Haemophilia A.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: April 04, 2025
Efficacy, safety, and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr8-1 trial.
Journal: Research and practice in thrombosis and haemostasis
Published: August 01, 2024
Valoctocogene roxaparvovec gene therapy provides durable haemostatic control for up to 7 years for haemophilia A.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: February 20, 2024
Three-year outcomes of valoctocogene roxaparvovec gene therapy for hemophilia A.
Journal: Journal of thrombosis and haemostasis : JTH
Published: November 03, 2023
Long-term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post-treatment.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: August 21, 2023
Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A.
Journal: The New England journal of medicine
Published: February 22, 2023
Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A.
Journal: The New England journal of medicine
Published: March 16, 2022
Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia A.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: March 02, 2021
Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A.
Journal: The New England journal of medicine
Published: January 02, 2020
Fibrinogen concentrate for treatment of bleeding and surgical prophylaxis in congenital fibrinogen deficiency patients.
Journal: Journal of thrombosis and haemostasis : JTH
Published: September 17, 2019
Real life experiences of a PK dosing study-Challenges and lessons learned.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: February 18, 2018
AAV5-Factor VIII Gene Transfer in Severe Hemophilia A.
Journal: The New England journal of medicine
Published: December 12, 2017
Last Updated: 09/26/2026