Bernadette Liemberger
Salzburg, 5020, Austria
Last Updated: 09/26/2026
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Found 12 publications
RiboScreenTM Technology Delivers Small-Molecule Ribodrugs to Convert Ribosomal Proteins into Molecular Valves for Tailored Protein Production Levels in Rare and Prevalent Disease †.
Journal: Biomedicines
Published: April 23, 2026
Prime editing as a promising therapeutic strategy for junctional epidermolysis bullosa.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: April 25, 2025
Splicing Modulation via Antisense Oligonucleotides in Recessive Dystrophic Epidermolysis Bullosa.
Journal: International journal of molecular sciences
Published: December 01, 2023
A Novel Fluorescence-Based Screen of Gene Editing Molecules for Junctional Epidermolysis Bullosa.
Journal: International journal of molecular sciences
Published: February 07, 2023
COL7A1 Editing via RNA Trans-Splicing in RDEB-Derived Skin Equivalents.
Journal: International journal of molecular sciences
Published: December 21, 2022
COL17A1 editing via homology-directed repair in junctional epidermolysis bullosa.
Journal: Frontiers in medicine
Published: June 23, 2022
Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: November 09, 2021
Personalized Development of Antisense Oligonucleotides for Exon Skipping Restores Type XVII Collagen Expression in Junctional Epidermolysis Bullosa.
Journal: International journal of molecular sciences
Published: February 26, 2021
A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa.
Journal: Molecular therapy. Nucleic acids
Published: December 14, 2020
Predictable CRISPR/Cas9-Mediated COL7A1 Reframing for Dystrophic Epidermolysis Bullosa.
Journal: The Journal of investigative dermatology
Published: September 23, 2019
Generation of rabbit polyclonal human and murine collagen VII monospecific antibodies: A useful tool for dystrophic epidermolysis bullosa therapy studies.
Journal: Matrix biology plus
Published: September 03, 2019
RNA Trans-Splicing Modulation via Antisense Molecule Interference.
Journal: International journal of molecular sciences
Published: January 30, 2018
Showing 1-12 of 12
Last Updated: 09/26/2026