Bernard Benichou
Paris, France
Last Updated: 09/26/2026
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Found 14 publications
Correction: VTX-PID as a novel recombinant immunoglobulin G-degrading enzyme (IdeS) for efficient AAV-based gene therapy in participants with neutralizing antibodies: results of the phase I first-in-human NAVIgATE study.
Journal: Frontiers in immunology
Published: June 03, 2026
VTX-PID as a novel recombinant immunoglobulin G-degrading enzyme (IdeS) for efficient AAV-based gene therapy in participants with neutralizing antibodies: results of the phase I first-in-human NAVIgATE study.
Journal: Frontiers in immunology
Published: March 06, 2026
From Radiocopper to Cold Copper: Mechanistic Modeling and Simulation to Define Clinical Response Criteria and Biomarkers for VTX-801 in Wilson Disease.
Journal: CPT: pharmacometrics & systems pharmacology
Published: August 08, 2025
Characteristics of patients with Wilson disease in the United States: An insurance claims database study.
Journal: World journal of hepatology
Published: October 10, 2023
Outcomes of 38 patients with PFIC3: Impact of genotype and of response to ursodeoxycholic acid therapy.
Journal: JHEP reports : innovation in hepatology
Published: April 26, 2023
Gene Therapy in Combination with Nitrogen Scavenger Pretreatment Corrects Biochemical and Behavioral Abnormalities of Infant Citrullinemia Type 1 Mice.
Journal: International journal of molecular sciences
Published: November 04, 2022
Epidemiology, treatment and burden of Wilson disease in France: A 10-year analysis of the national health insurance database.
Journal: Clinics and research in hepatology and gastroenterology
Published: March 21, 2022
High value of 64Cu as a tool to evaluate the restoration of physiological copper excretion after gene therapy in Wilson's disease.
Journal: Molecular therapy. Methods & clinical development
Published: November 10, 2021
Optimising the IgG-degrading enzyme treatment regimen for enhanced adeno-associated virus transduction in the presence of neutralising antibodies.
Journal: Clinical & translational immunology
Published: June 18, 2021
Gene therapy for progressive familial intrahepatic cholestasis type 3 in a clinically relevant mouse model.
Journal: Nature communications
Published: December 21, 2018
Low-dose agalsidase beta treatment in male pediatric patients with Fabry disease: A 5-year randomized controlled trial.
Journal: Molecular genetics and metabolism
Published: December 13, 2018
Liver Expression of a MiniATP7B Gene Results in Long-Term Restoration of Copper Homeostasis in a Wilson Disease Model in Mice.
Journal: Hepatology (Baltimore, Md.)
Published: July 13, 2018
Last Updated: 09/26/2026