Last Updated: 09/26/2026
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Found 26 publications
Cardiotoxic Effects and Microdystrophin Expression after Gene Therapy for DMD.
Journal: The New England journal of medicine
Published: July 22, 2026
Diagnosis of platelet dysfunction in children: clinical predictors and test methods.
Journal: Blood vessels, thrombosis & hemostasis
Published: May 22, 2025
Use of CD19-targeted immune modulation to eradicate AAV-neutralizing antibodies.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: December 06, 2024
Intron 22 inversions: cross-reactive material or no cross-reactive material?
Journal: Journal of thrombosis and haemostasis : JTH
Published: August 19, 2024
Coagulation factor VIII: biological basis of emerging hemophilia A therapies.
Journal: Blood
Published: May 07, 2024
AAV gene therapy in companion dogs with severe hemophilia: Real-world long-term data on immunogenicity, efficacy, and quality of life.
Journal: Molecular therapy. Methods & clinical development
Published: October 18, 2023
Enhanced procoagulant activity of select hemophilia B causing factor IX variants with emicizumab.
Journal: Blood
Published: July 21, 2023
Analysis of vector genome integrations in multicentric lymphoma after AAV gene therapy in a severe hemophilia A dog.
Journal: Molecular therapy. Methods & clinical development
Published: June 16, 2023
Coagulation factor VIII regulates von Willebrand factor homeostasis invivo.
Journal: Journal of thrombosis and haemostasis : JTH
Published: June 16, 2023
Acquired Hemophilia A: Current Guidance and Experience from Clinical Practice.
Journal: Journal of blood medicine
Published: January 29, 2022
Last Updated: 09/26/2026