Blair R. Leavitt
Vancouver, BC, Canada
Last Updated: 09/26/2026
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Found 152 publications
Preface to special issue on neurodevelopment in Huntington's disease.
Journal: Journal of Huntington's disease
Published: May 27, 2026
Wild-type huntingtin in neurodevelopment.
Journal: Journal of Huntington's disease
Published: April 09, 2026
Humanized mice carrying a pathogenic GRN deletion as a pre-clinical platform for targeted gene therapies in frontotemporal dementia.
Journal: Neurobiology of disease
Published: March 06, 2026
Silencing of human HTT by targeted CRISPR/dCas9-mediated epigenetic editing.
Journal: Journal of Huntington's disease
Published: January 22, 2026
Classical and Emerging Biomarkers in Pyridoxine-Dependent Epilepsy (PDE-ALDH7A1): Implications for Early Diagnosis and Therapeutic Development.
Journal: Biomolecules
Published: December 28, 2025
Design and development of lipid nanoparticle formulations for brain gene therapy.
Journal: Molecular therapy. Nucleic acids
Published: August 19, 2025
Oral splicing modulator branaplam in Huntington's disease: a phase 2 randomized controlled trial.
Journal: Nature medicine
Published: June 16, 2025
Quantitative relationship between tominersen concentrations in cerebrospinal fluid and biomarker changes in Huntington's disease patients.
Journal: British journal of clinical pharmacology
Published: June 10, 2025
Targeting AASS alleviates neurotoxicity and improves mitochondrial function in astrocyte models for pyridoxine-dependent epilepsy.
Journal: Molecular therapy. Nucleic acids
Published: April 09, 2025
Emerging roles of microglia and neuroinflammation in Huntington's disease: From pathophysiology to clinical trials.
Journal: Journal of Huntington's disease
Published: March 28, 2025
Last Updated: 09/26/2026