Last Updated: 09/26/2026
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Found 36 publications
Evaluation of One-Stage Assays for the Monitoring of Recombinant Human Factor IX Padua Activity After Etranacogene Dezaparvovec Gene Therapy.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: December 12, 2024
Sex-specific NLRP3 activation in neutrophils promotes neutrophil recruitment and NETosis in the murine model of diffuse alveolar hemorrhage.
Journal: Frontiers in immunology
Published: July 17, 2024
Risk of Intracranial Hemorrhage in Persons with Hemophilia A in the United States: Real-World Retrospective Cohort Study Using the ATHNdataset.
Journal: Journal of blood medicine
Published: November 15, 2023
Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial.
Journal: The Lancet. Haematology
Published: October 04, 2023
Immunogenicity, safety, and efficacy of rurioctocog alfa pegol in previously untreated patients with severe hemophilia A: interim results from a phase 3, prospective, multicenter, open-label study.
Journal: Expert review of hematology
Published: August 30, 2023
Inhibition of protein arginine deiminase 4 prevents inflammation-mediated heart failure in arthritis.
Journal: Life science alliance
Published: March 23, 2023
Building the foundation for a community-generated national research blueprint for inherited bleeding disorders: facilitating research through infrastructure, workforce, resources and funding.
Journal: Expert review of hematology
Published: March 15, 2023
Evaluation of collagen turnover biomarkers as an objective measure for efficacy of treatment with rurioctocog alfa pegol in patients with hemophilia A: a secondary analysis of a randomized controlled trial.
Journal: Journal of thrombosis and haemostasis : JTH
Published: October 03, 2022
Structure and Function of Recombinant versus Plasma-Derived von Willebrand Factor and Impact on Multimer Pharmacokinetics in von Willebrand Disease.
Journal: Journal of blood medicine
Published: June 17, 2022
Economic Burden Associated with Major Surgery in Patients with von Willebrand Disease: A United States Retrospective Administrative Database Analysis.
Journal: Journal of blood medicine
Published: May 19, 2021
Economic burden of major bleeding events in commercially insured patients with von Willebrand disease based on claims data from the United States.
Journal: Journal of managed care & specialty pharmacy
Published: December 14, 2020
Psychometric evaluation of a patient-reported outcomes instrument for congenital thrombotic thrombocytopenic purpura.
Journal: Journal of patient-reported outcomes
Published: December 08, 2020
Last Updated: 09/26/2026