Carla J. Jonker

Utrecht, UT, Netherlands

Last Updated: 09/26/2026

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Found 14 publications

Corrigendum to "Learnings from a registry-based cohort study for spinal muscular atrophy disease" [Neuromuscular Disorders, Volume 59, February 2026, 106332].

Corrigendum to "Learnings from a registry-based cohort study for spinal muscular atrophy disease" [Neuromuscular Disorders, Volume 59, February 2026, 106332].

Journal: Neuromuscular disorders : NMD

Published: March 28, 2026

Learnings from a registry-based cohort study for spinal muscular atrophy disease.

Learnings from a registry-based cohort study for spinal muscular atrophy disease.

Journal: Neuromuscular disorders : NMD

Published: June 20, 2025

Optimizing Patient Registries for Regulatory Decision Making - Key Learnings From an HMA/EMA Multistakeholder Workshop.

Optimizing Patient Registries for Regulatory Decision Making - Key Learnings From an HMA/EMA Multistakeholder Workshop.

Journal: Clinical pharmacology and therapeutics

Published: December 05, 2024

Framework for Multistakeholder Patient Registries in the Field of Rare Diseases: Focus on Neurogenetic Diseases.

Framework for Multistakeholder Patient Registries in the Field of Rare Diseases: Focus on Neurogenetic Diseases.

Journal: Neurology

Published: August 22, 2024

Learning from European regulator-initiated studies for regulatory decision making.

Learning from European regulator-initiated studies for regulatory decision making.

Journal: Drug discovery today

Published: January 24, 2024

Real world evidence: Perspectives from a European Society of Cardiology Cardiovascular Round Table with contribution from the European Medicines Agency.

Real world evidence: Perspectives from a European Society of Cardiology Cardiovascular Round Table with contribution from the European Medicines Agency.

Journal: European heart journal. Quality of care & clinical outcomes

Published: December 23, 2022

Contribution of Real-World Evidence in European Medicines Agency's Regulatory Decision Making.

Contribution of Real-World Evidence in European Medicines Agency's Regulatory Decision Making.

Journal: Clinical pharmacology and therapeutics

Published: August 17, 2022

Collection of Data on Adverse Events Related to Medicinal Products: A Survey Among Registries in the ENCePP Resources Database.

Collection of Data on Adverse Events Related to Medicinal Products: A Survey Among Registries in the ENCePP Resources Database.

Journal: Drug safety

Published: May 10, 2022

Contribution of patient registries to regulatory decision making on rare diseases medicinal products in Europe.

Contribution of patient registries to regulatory decision making on rare diseases medicinal products in Europe.

Journal: Frontiers in pharmacology

Published: April 20, 2022

Capturing Data in Rare Disease Registries to Support Regulatory Decision Making: A Survey Study Among Industry and Other Stakeholders.

Capturing Data in Rare Disease Registries to Support Regulatory Decision Making: A Survey Study Among Industry and Other Stakeholders.

Journal: Drug safety

Published: May 16, 2021

Inhibitor development in previously untreated patients with severe haemophilia: A comparison of included patients and outcomes between a clinical study and a registry-based study.

Inhibitor development in previously untreated patients with severe haemophilia: A comparison of included patients and outcomes between a clinical study and a registry-based study.

Journal: Haemophilia : the official journal of the World Federation of Hemophilia

Published: December 20, 2019

Drug Registries and Approval of Drugs: Promises, Placebo, or a Real Success?

Drug Registries and Approval of Drugs: Promises, Placebo, or a Real Success?

Journal: Clinical therapeutics

Published: January 24, 2018

Showing 1-12 of 14

Last Updated: 09/26/2026