Caroline Le Guiner

Nantes, France

Last Updated: 09/26/2026

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Found 42 publications

Spontaneous rhabdomyosarcomas in Dmdmdx rats.

Spontaneous rhabdomyosarcomas in Dmdmdx rats.

Journal: Veterinary pathology

Published: June 30, 2026

Transcriptomic profiling of skeletal muscle in the DMDmdx rat model of Duchenne muscular dystrophy.

Transcriptomic profiling of skeletal muscle in the DMDmdx rat model of Duchenne muscular dystrophy.

Journal: Scientific reports

Published: May 07, 2025

Dose- and genotype-dependent cardiac arrhythmia and sudden death in rats following microdystrophin gene therapy.

Dose- and genotype-dependent cardiac arrhythmia and sudden death in rats following microdystrophin gene therapy.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: March 15, 2025

Early Endosome Disturbance and Endolysosomal Pathway Dysfunction in Duchenne Muscular Dystrophy.

Early Endosome Disturbance and Endolysosomal Pathway Dysfunction in Duchenne Muscular Dystrophy.

Journal: The American journal of pathology

Published: January 10, 2025

Advancing liver gene therapy: Enhanced transduction with GalNAc-bioconjugated rAAV capsids.

Advancing liver gene therapy: Enhanced transduction with GalNAc-bioconjugated rAAV capsids.

Journal: Biomedicine & pharmacotherapy = Biomedecine & pharmacotherapie

Published: August 19, 2024

Dystrophin deficiency impairs cell junction formation during embryonic myogenesis.

Dystrophin deficiency impairs cell junction formation during embryonic myogenesis.

Journal: bioRxiv : the preprint server for biology

Published: December 18, 2023

Novel chemical tyrosine functionalization of adeno-associated virus improves gene transfer efficiency in liver and retina.

Novel chemical tyrosine functionalization of adeno-associated virus improves gene transfer efficiency in liver and retina.

Journal: Biomedicine & pharmacotherapy = Biomedecine & pharmacotherapie

Published: November 07, 2023

Dystrophin deficiency impairs cell junction formation during embryonic myogenesis from pluripotent stem cells.

Dystrophin deficiency impairs cell junction formation during embryonic myogenesis from pluripotent stem cells.

Journal: iScience

Published: October 09, 2023

Mannose-coupled AAV2: A second-generation AAV vector for increased retinal gene therapy efficiency.

Mannose-coupled AAV2: A second-generation AAV vector for increased retinal gene therapy efficiency.

Journal: Molecular therapy. Methods & clinical development

Published: December 14, 2022

Muscle Pathology in Dystrophic Rats and Zebrafish Is Unresponsive to Taurine Treatment, Compared to the mdx Mouse Model for Duchenne Muscular Dystrophy.

Muscle Pathology in Dystrophic Rats and Zebrafish Is Unresponsive to Taurine Treatment, Compared to the mdx Mouse Model for Duchenne Muscular Dystrophy.

Journal: Metabolites

Published: November 30, 2022

Intravitreal air tamponade after AAV2 subretinal injection modifies retinal EGFP distribution.

Intravitreal air tamponade after AAV2 subretinal injection modifies retinal EGFP distribution.

Journal: Molecular therapy. Methods & clinical development

Published: November 03, 2022

Evaluation of an AAV9-mini-dystrophin gene therapy candidate in a rat model of Duchenne muscular dystrophy.

Evaluation of an AAV9-mini-dystrophin gene therapy candidate in a rat model of Duchenne muscular dystrophy.

Journal: Molecular therapy. Methods & clinical development

Published: July 29, 2022

Showing 1-12 of 42

Last Updated: 09/26/2026