Charlotte M. Rasmussen
Odense C, 5000, Denmark
Last Updated: 09/26/2026
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Found 9 publications
Correction: Reporting preclinical gene therapy studies in the field of Niemann-Pick type C disease according to the ARRIVE guidelines.
Journal: Orphanet journal of rare diseases
Published: June 10, 2025
The oral bioavailability of a pleuromutilin antibiotic candidate is increased after co-administration with the CYP3A4 inhibitor ritonavir and the P-gp inhibitor zosuquidar formulated as amorphous solid dispersions.
Journal: International journal of pharmaceutics
Published: January 10, 2025
Endothelial and neuronal engagement by AAV-BR1 gene therapy alleviates neurological symptoms and lipid deposition in a mouse model of Niemann-Pick type C2.
Journal: Fluids and barriers of the CNS
Published: October 11, 2024
Upregulation of Transferrin Receptor 1 (TfR1) but Not Glucose Transporter 1 (GLUT1) or CD98hc at the Blood-Brain Barrier in Response to Valproic Acid.
Journal: Cells
Published: April 26, 2024
Reporting preclinical gene therapy studies in the field of Niemann-Pick type C disease according to the ARRIVE guidelines.
Journal: Orphanet journal of rare diseases
Published: March 20, 2024
The Npc2Gt(LST105)BygNya mouse signifies pathological changes comparable to human Niemann-Pick type C2 disease.
Journal: Molecular and cellular neurosciences
Published: March 17, 2023
Edge artificial intelligence wireless video capsule endoscopy.
Journal: Scientific reports
Published: January 20, 2022
A novel strategy for delivering Niemann-Pick type C2 proteins across the blood-brain barrier using the brain endothelial-specific AAV-BR1 virus.
Journal: Journal of neurochemistry
Published: January 19, 2022
Showing 1-9 of 9
Last Updated: 09/26/2026