Christine Rivat
London, ENG WC1A2SL, United Kingdom
Last Updated: 09/26/2026
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Found 16 publications
Effect of vosoritide on spine morphology in children with achondroplasia: 1-year results from a randomized phase 2 study.
Journal: Journal of the Endocrine Society
Published: October 15, 2025
Effect of vosoritide on genu varum in children with achondroplasia after 1 year in randomized placebo-controlled trials.
Journal: Journal of the Endocrine Society
Published: October 15, 2025
Efficacy, safety, and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr8-1 trial.
Journal: Research and practice in thrombosis and haemostasis
Published: August 01, 2024
Author Correction: Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndrome.
Journal: Nature medicine
Published: August 09, 2022
Clonal expansion of T memory stem cells determines early anti-leukemic responses and long-term CAR T cell persistence in patients.
Journal: Nature cancer
Published: August 04, 2021
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
Journal: The New England journal of medicine
Published: May 11, 2021
Preclinical Optimization and Safety Studies of a New Lentiviral Gene Therapy for p47phox-Deficient Chronic Granulomatous Disease.
Journal: Human gene therapy
Published: March 20, 2021
Long-term lymphoid progenitors independently sustain naïve T and NK cell production in humans.
Journal: Nature communications
Published: August 06, 2020
Lentiviral gene therapy for X-linked chronic granulomatous disease.
Journal: Nature medicine
Published: July 18, 2019
Gene therapy for Wiskott-Aldrich syndrome in a severely affected adult.
Journal: Blood
Published: April 04, 2017
Molecular remission of infant B-ALL after infusion of universal TALEN gene-edited CAR T cells.
Journal: Science translational medicine
Published: July 08, 2016
Last Updated: 09/26/2026