Christoph Wandel
Basel, BS, Switzerland
Last Updated: 09/26/2026
Save publications for later
Sign Up
Not sure about your diagnosis?
Check Your Symptoms
Found 20 publications
Cardiac Safety Outcomes in Delandistrogene Moxeparvovec Clinical Trials for Duchenne Muscular Dystrophy with Up to 5 Years of Follow-up.
Journal: Cardiology and therapy
Published: April 03, 2026
Immunologic investigations into transgene directed immune-mediated myositis following delandistrogene moxeparvovec gene therapy.
Journal: Scientific reports
Published: June 11, 2024
AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial.
Journal: Nature medicine
Published: March 22, 2024
Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to <8 Years) with Duchenne Muscular Dystrophy: 1-Year Interim Results from Study SRP-9001-103 (ENDEAVOR).
Journal: Annals of neurology
Published: February 02, 2023
A randomized, double-blind, placebo-controlled phase II trial to explore the effects of a GABAA-α5 NAM (basmisanil) on intellectual disability associated with Down syndrome.
Journal: Journal of neurodevelopmental disorders
Published: August 10, 2021
Efficacy and safety of balovaptan for socialisation and communication difficulties in autistic adults in North America and Europe: a phase 3, randomised, placebo-controlled trial.
Journal: The lancet. Psychiatry
Published: July 14, 2021
Bioavailability and pharmacokinetic profile of balovaptan, a selective, brain-penetrant vasopressin 1a receptor antagonist, in healthy volunteers.
Journal: Expert opinion on investigational drugs
Published: June 28, 2021
Basmisanil, a highly selective GABAA-α5 negative allosteric modulator: preclinical pharmacology and demonstration of functional target engagement in man.
Journal: Scientific reports
Published: October 09, 2020
PKPD and cardiac single cell modeling of a DDI study with a CYP3A4 substrate and itraconazole to quantify the effects on QT interval duration.
Journal: Journal of pharmacokinetics and pharmacodynamics
Published: March 13, 2019
Last Updated: 09/26/2026