Last Updated: 09/26/2026
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Found 205 publications
Cardiac Safety Outcomes in Delandistrogene Moxeparvovec Clinical Trials for Duchenne Muscular Dystrophy with Up to 5 Years of Follow-up.
Journal: Cardiology and therapy
Published: April 03, 2026
Deramiocel heart-derived cellular therapy in advanced Duchenne muscular dystrophy (HOPE-3): a phase 3, randomised, double-blind, placebo-controlled trial.
Journal: Lancet (London, England)
Published: March 26, 2026
Learnings from Patient Mortality after Delandistrogene Moxeparvovec Administration: A Report of Two Cases and Expert Committee Considerations for Future Mitigation and Management.
Journal: Human gene therapy
Published: February 13, 2026
Leading the Way: Cellular and Gene Therapies in Physical Medicine and Rehabilitation Transforming Functional Outcomes Through Regenerative Innovation.
Journal: American journal of physical medicine & rehabilitation
Published: February 08, 2026
Descriptive characterization of ambulatory health states in Duchenne muscular dystrophy: Motor function trajectories and times to loss of ambulation.
Journal: Journal of neuromuscular diseases
Published: September 23, 2025
Two-Year Outcomes Following Delandistrogene Moxeparvovec Treatment in Ambulatory Patients with Duchenne Muscular Dystrophy: Phase 3 EMBARK Trial.
Journal: Neurology and therapy
Published: September 10, 2025
Confirmatory long-term efficacy and safety results of ataluren in patients with nmDMD from Study 041, an international, randomized, double-blind, placebo-controlled, Phase III trial.
Journal: Journal of comparative effectiveness research
Published: August 22, 2025
Association between exon-skipping therapy with eteplirsen and cardiac outcomes in Duchenne muscular dystrophy.
Journal: Journal of neuromuscular diseases
Published: August 20, 2025
Exposure-response of serum biomarkers to vamorolone, a dissociative corticosteroidal anti-inflammatory drug, in 4- to <7-year children.
Journal: Steroids
Published: August 11, 2025
Home-Based Exercise Improves Muscle Oxidative Capacity in Kidney Disease.
Journal: Kidney international reports
Published: June 25, 2025
Last Updated: 09/26/2026