Last Updated: 09/26/2026
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Found 9 publications
A prospective short-term study to evaluate methodologies for the assessment of disease extent, impact, and wound evolution in patients with dystrophic epidermolysis bullosa.
Journal: Orphanet journal of rare diseases
Published: December 20, 2021
A systematic literature review of the disease burden in patients with recessive dystrophic epidermolysis bullosa.
Journal: Orphanet journal of rare diseases
Published: December 03, 2020
Long-term safety and sustained efficacy for up to 5 years of treatment with recombinant factor IX Fc fusion protein in subjects with haemophilia B: Results from the B-YOND extension study.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: December 23, 2019
Recombinant factor VIII Fc fusion protein for the treatment of severe haemophilia A: Final results from the ASPIRE extension study.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: November 25, 2019
Impact of hepatic and renal impairment on the pharmacokinetics and tolerability of eliglustat therapy for Gaucher disease type 1.
Journal: Molecular genetics and metabolism
Published: May 16, 2019
First-in-human, randomized dose-escalation study of the safety, tolerability, pharmacokinetics, pharmacodynamics and immunogenicity of PF-06480605 in healthy subjects.
Journal: British journal of clinical pharmacology
Published: April 29, 2019
Inadequacy of current pediatric epinephrine autoinjector needle length for use in infants and toddlers.
Journal: Annals of allergy, asthma & immunology : official publication of the American College of Allergy, Asthma, & Immunology
Published: November 29, 2016
A randomized phase 1 pharmacokinetic trial comparing the potential biosimilar PF-05280014 with trastuzumab in healthy volunteers (REFLECTIONS B327-01).
Journal: British journal of clinical pharmacology
Published: February 21, 2014
Evaluation of the effect of food and ketoconazole on the pharmacokinetics of the smoothened inhibitor PF-04449913 in healthy volunteers.
Journal: Cancer chemotherapy and pharmacology
Published: December 12, 2013
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Last Updated: 09/26/2026