Last Updated: 09/26/2026
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Found 125 publications
Genetic Medicine - Primed and Ready.
Journal: The New England journal of medicine
Published: March 25, 2026
Analysing long-read CRISPR experiments with CRISPRLungo.
Journal: Nature biomedical engineering
Published: November 24, 2025
Analyzing long-read CRISPR experiments with CRISPRLungo.
Journal: bioRxiv : the preprint server for biology
Published: November 24, 2025
Modular Platform for Therapeutic Drug Delivery Using Trifunctional Bio-Orthogonal Macromolecular Conjugates.
Journal: Bioconjugate chemistry
Published: November 10, 2025
Nucleotide-resolution mapping of regulatory elements via allelic readout of tiled base editing.
Journal: Nature communications
Published: October 27, 2025
Direct and indirect regulation of fetal globin transcript by RNA-binding protein IGF2BP1.
Journal: Blood
Published: September 26, 2025
Direct and indirect regulation of fetal globin transcript by RNA-binding protein IGF2BP1.
Journal: bioRxiv : the preprint server for biology
Published: September 18, 2025
A xeno-free red blood cell differentiation formula models sickle cell disease from somatically sourced patient iPSCs.
Journal: Experimental hematology
Published: September 07, 2025
Modular platform for therapeutic drug delivery using trifunctional bio-orthogonal macromolecular conjugates.
Journal: bioRxiv : the preprint server for biology
Published: August 08, 2025
In cellulo DNA assembly for targeted genomic integration and rearrangement in human cells.
Journal: bioRxiv : the preprint server for biology
Published: July 16, 2025
CRISPR-based therapeutic genome editing for inherited blood disorders.
Journal: Nature reviews. Drug discovery
Published: June 03, 2025
In situ gene editing of hematopoietic stem cells via AAV-delivered CRISPR guide RNAs.
Journal: Blood advances
Published: April 11, 2025
Last Updated: 09/26/2026