Diana D. Lobo
Coimbra, Portugal
Last Updated: 09/26/2026
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Found 12 publications
Innate Immunocompetent hiPSC-Derived Neurospheroids Capture Early CNS Responses to rAAV.
Journal: Advanced science (Weinheim, Baden-Wurttemberg, Germany)
Published: October 15, 2025
Spinocerebellar ataxia type 3: from pathogenesis to promising therapeutics.
Journal: Trends in molecular medicine
Published: May 01, 2025
Circadian rhythms are disrupted in patients and preclinical models of Machado-Joseph disease.
Journal: Brain : a journal of neurology
Published: January 03, 2025
Extracellular vesicles-associated AAVs for the treatment of Machado-Joseph disease.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: October 03, 2024
Isolation of Adeno-associated Viral Vectors Through a Single-step and Semi-automated Heparin Affinity Chromatography Protocol.
Journal: Journal of visualized experiments : JoVE
Published: April 22, 2024
A systematic screening assay identifies efficient small guide RNAs for CRISPR activation.
Journal: Frontiers in bioengineering and biotechnology
Published: November 10, 2023
Viral-based animal models in polyglutamine disorders.
Journal: Brain : a journal of neurology
Published: July 09, 2023
Extracellular vesicle-based delivery of silencing sequences for the treatment of Machado-Joseph disease/spinocerebellar ataxia type 3.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: October 30, 2022
miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3.
Journal: Nucleic acid therapeutics
Published: December 08, 2021
ULK overexpression mitigates motor deficits and neuropathology in mouse models of Machado-Joseph disease.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: December 19, 2020
Antisense oligonucleotide therapeutics in neurodegenerative diseases: the case of polyglutamine disorders.
Journal: Brain : a journal of neurology
Published: February 07, 2019
Showing 1-12 of 12
Last Updated: 09/26/2026