Elena Draghici

Milan, Italy

Last Updated: 09/26/2026

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Found 15 publications

A standardized protocol for assessing immunodeficiency in mouse models.

A standardized protocol for assessing immunodeficiency in mouse models.

Journal: Veterinary pathology

Published: August 28, 2025

Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency.

Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency.

Journal: Science translational medicine

Published: February 07, 2024

Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations.

Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations.

Journal: Frontiers in immunology

Published: July 28, 2023

Thymic Epithelial Cell Alterations and Defective Thymopoiesis Lead to Central and Peripheral Tolerance Perturbation in MHCII Deficiency.

Thymic Epithelial Cell Alterations and Defective Thymopoiesis Lead to Central and Peripheral Tolerance Perturbation in MHCII Deficiency.

Journal: Frontiers in immunology

Published: February 19, 2021

Efficacy and safety of anti-CD45-saporin as conditioning agent for RAG deficiency.

Efficacy and safety of anti-CD45-saporin as conditioning agent for RAG deficiency.

Journal: The Journal of allergy and clinical immunology

Published: January 28, 2020

Expanded circulating hematopoietic stem/progenitor cells as novel cell source for the treatment of TCIRG1 osteopetrosis.

Expanded circulating hematopoietic stem/progenitor cells as novel cell source for the treatment of TCIRG1 osteopetrosis.

Journal: Haematologica

Published: September 14, 2019

Gene Modification and Three-Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches.

Gene Modification and Three-Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches.

Journal: Stem cells translational medicine

Published: October 08, 2018

Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation.

Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation.

Journal: The Journal of allergy and clinical immunology

Published: May 15, 2017

Autonomous role of Wiskott-Aldrich syndrome platelet deficiency in inducing autoimmunity and inflammation.

Autonomous role of Wiskott-Aldrich syndrome platelet deficiency in inducing autoimmunity and inflammation.

Journal: The Journal of allergy and clinical immunology

Published: March 23, 2017

Good Laboratory Practice Preclinical Safety Studies for GSK2696273 (MLV Vector-Based Ex Vivo Gene Therapy for Adenosine Deaminase Deficiency Severe Combined Immunodeficiency) in NSG Mice.

Good Laboratory Practice Preclinical Safety Studies for GSK2696273 (MLV Vector-Based Ex Vivo Gene Therapy for Adenosine Deaminase Deficiency Severe Combined Immunodeficiency) in NSG Mice.

Journal: Human gene therapy. Clinical development

Published: March 21, 2017

In Vivo Chronic Stimulation Unveils Autoreactive Potential of Wiskott-Aldrich Syndrome Protein-Deficient B Cells.

In Vivo Chronic Stimulation Unveils Autoreactive Potential of Wiskott-Aldrich Syndrome Protein-Deficient B Cells.

Journal: Frontiers in immunology

Published: February 09, 2017

Development of central nervous system autoimmunity is impaired in the absence of Wiskott-Aldrich syndrome protein.

Development of central nervous system autoimmunity is impaired in the absence of Wiskott-Aldrich syndrome protein.

Journal: PloS one

Published: August 30, 2013

Showing 1-12 of 15

Last Updated: 09/26/2026