Last Updated: 09/26/2026
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Found 2 publications
Gene therapy for hemophilia B: results from the phase 1/2 101HEMB01/02 studies.
Journal: Blood advances
Published: October 29, 2024
Safety and Efficacy of DTX401, an AAV8-Mediated Liver-Directed Gene Therapy, in Adults With Glycogen Storage Disease Type I a (GSDIa).
Journal: Journal of inherited metabolic disease
Published: October 08, 2024
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Last Updated: 09/26/2026